Hemophilia Clinical Trials in Los Angeles, California
9 recruitingLos Angeles, California
Showing 1–9 of 9 trials
Recruiting
Phase 3
A Study to Investigate the Efficacy and Safety of Fitusiran Prophylaxis in Male Participants Aged 1 to Less Than 12 Years With Hemophilia A or B
Hemophilia
Sanofi85 enrolled21 locationsNCT07285460
Recruiting
Phase 1Phase 2
A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B
Hemophilia B
Regeneron Pharmaceuticals130 enrolled41 locationsNCT06379789
Recruiting
Pharmacokinetics, Pharmacodynamics, and Safety Profile of Understudied Drugs Administered to Children Per Standard of Care (POPS)
Heart FailurePainInsomnia+22 more
Duke University5,000 enrolled51 locationsNCT04278404
Recruiting
Phase 1
A Study to Learn About How Changing Therapy From Emicizumab to Marstacimab Affects People With the Severe Hemophilia A.
Severe Hemophilia A
Pfizer15 enrolled4 locationsNCT06703606
Recruiting
Phase 1
A Study of Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of SR604 in Two Participants Groups (Part A: Healthy Participants, and Part B: Participants With Hemophilia A or Hemophilia B or Factor VII Deficiency)
Healthy ParticipantsHemophilia AHemophilia B+1 more
Equilibra Bioscience LLC31 enrolled10 locationsNCT06349473
Recruiting
Phase 4
SEVENFACT® for Bleeding Events in Hemophilia With Inhibitors
Hemophilia A With InhibitorHemophilia B With Inhibitor
American Thrombosis and Hemostasis Network55 enrolled21 locationsNCT04647227
Recruiting
ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders
ThrombophiliaThrombosisSickle Cell Disease+10 more
American Thrombosis and Hemostasis Network3,000 enrolled71 locationsNCT04398628
Recruiting
Phase 4
A Study to Test a Medicine (Fitusiran) for Preventing Bleeds in People With Severe Hemophilia Who Previously Received Preventive Treatment With Emicizumab
Hemophilia A
Sanofi20 enrolled2 locationsNCT06145373
Recruiting
Effects of Emicizumab vs. Factor VIII Prophylaxis on Joint and Bone Health in Severe Hemophilia A
Hemophilia A
Washington Institute for Coagulation40 enrolled4 locationsNCT04131036