Phase 1 Hereditary hemorrhagic telangiectasia Clinical Trials
5 recruitingPhase 1
What is a Phase 1 trial?
Phase 1 trials test a new treatment in a small group of people for the first time. The primary goal is to evaluate safety, determine a safe dosage range, and identify side effects. These studies typically enroll 20 to 80 participants.
Showing 1–5 of 5 trials
Recruiting
Phase 1Phase 2
DIAG723 in Adults With Hereditary Hemorrhagic Telangiectasia
Pulmonary Arterial HypertensionHereditary hemorrhagic telangiectasia
Diagonal Therapeutics, Inc.93 enrolled5 locationsNCT07623525
Recruiting
Phase 1
Topical TOR-582 Treatment of Epistaxis in HHT
EpistaxisHereditary Hemorrhagic Telangiectasia (HHT)
Columbia University27 enrolled1 locationNCT07667413
Recruiting
Phase 1Phase 2
A Study to Evaluate ALN-6400 in Healthy Volunteers and Patients With Hereditary Hemorrhagic Telangiectasia (HHT)
Hereditary hemorrhagic telangiectasia
Alnylam Pharmaceuticals120 enrolled16 locationsNCT06659640
Recruiting
Phase 1
A single ascending dose study of TX002100 in healthy participants
Hereditary hemorrhagic telangiectasia
Tectonic Operating Company. Inc.48 enrolled1 locationACTRN12626000242325
Recruiting
Phase 1
A Trial of TER-1754 in Patients With Hereditary Hemorrhagic Telangiectasia
Hereditary Hemorrhagic Telangiectasia (HHT)
Terremoto Biosciences Inc.90 enrolled1 locationNCT07255846