Idiopathic Short Stature Clinical Trials

7 recruitingLast updated: June 18, 2026

There are 7 actively recruiting idiopathic short stature clinical trials across 8 countries. Studies span Phase 3, Not Applicable, Phase 2. Top locations include Sacramento, California, United States, New Orleans, Louisiana, United States, Idaho Falls, Idaho, United States. Updated daily from ClinicalTrials.gov.


Idiopathic Short Stature Trials at a Glance

7 actively recruiting trials for idiopathic short stature are listed on ClinicalTrialsFinder across 6 cities in 8 countries. The largest study group is Phase 3 with 2 trials, with the heaviest enrollment activity in Sacramento, New Orleans, and Idaho Falls. Lead sponsors running idiopathic short stature studies include BioMarin Pharmaceutical, Ascendis Pharma A/S, and Dong-A ST Co., Ltd..

Browse idiopathic short stature trials by phase

Treatments under study

About Idiopathic Short Stature Clinical Trials

Looking for clinical trials for Idiopathic Short Stature? There are currently 7 studies actively recruiting participants. Clinical trials offer access to new treatments before they are widely available, and every approved therapy in use today was first tested through a clinical trial.

Below you can browse trials, sign up for alerts when new Idiopathic Short Stature trials open, and view eligibility criteria for each study. Each listing includes the study phase, locations, and enrollment details.

Frequently Asked Questions

Common questions about Idiopathic Short Stature clinical trials

A clinical trial is a carefully designed research study that tests new medical treatments, drugs, devices, or approaches in human volunteers. Every approved medication and treatment available today was proven safe and effective through clinical trials.

All clinical trials are reviewed and approved by Institutional Review Boards (IRBs) — independent committees that evaluate patient safety. Trials follow strict protocols, and your health is monitored closely throughout. You can withdraw at any time.

Not necessarily. Many trials compare the new treatment against the current standard of care, meaning all participants receive active treatment. When placebos are used, they are typically combined with standard treatment, not given alone. The trial description will always specify the design.

Under the Affordable Care Act, most private insurers are required to cover routine patient care costs during a clinical trial. The sponsor typically covers the investigational treatment itself. Medicare also covers routine costs for qualifying trials.

Yes. Participation is completely voluntary. You can withdraw at any time, for any reason, without it affecting your access to standard medical care.

Each trial has specific eligibility criteria — including age, diagnosis, disease stage, prior treatments, and general health. Browse the trials listed above and check their eligibility sections. You can also contact the trial site directly to discuss your situation.

Showing 17 of 7 trials

Recruiting
Phase 3

Trial Investigating the Efficacy and Safety of Weekly Lonapegsomatropin Compared to Daily Somatropin in Children and Adolescents With Short Stature or Growth Failure Due to Growth Hormone Sufficient Disorders

Turner SyndromeIdiopathic Short StatureShort Stature Homeobox Gene Mutation+1 more
Ascendis Pharma A/S186 enrolled19 locationsNCT07221851
Recruiting
Phase 2

A Phase 2 Study of Vosoritide in Children With Idiopathic Short Stature

Idiopathic Short Stature
BioMarin Pharmaceutical100 enrolled47 locationsNCT06382155
Recruiting
Not Applicable

Multidisciplinary Evaluation and a Genome-wide Analysis in a Cohort of Idiopathic Short Stature Patients

Idiopathic Short Stature
University Hospital, Montpellier200 enrolled1 locationNCT05858606
Recruiting
Phase 3

The Efficacy and Safety of Inpegsomatropin Injection in Children With Idiopathic Short Stature

Idiopathic Short Stature
Xiamen Amoytop Biotech Co., Ltd.300 enrolled38 locationsNCT06927310
Recruiting

A Study to Assess Growth in Children With Idiopathic Short Stature

Idiopathic Short Stature
BioMarin Pharmaceutical300 enrolled40 locationsNCT06309979
Recruiting

Long-term Safety and Effectiveness of Growtropin®-II Treatment in Children With Short Stature

Turner SyndromeGrowth Hormone DeficiencySmall for Gestational Age+1 more
Dong-A ST Co., Ltd.2,500 enrolled1 locationNCT04798690
Recruiting

Long-term Safety and Effectiveness of Growth Hormone With GHD, TS, CRF, SGA , ISS and PWS in Children

Turner SyndromeChronic Renal FailureGrowth Hormone Deficiency+2 more
LG Chem6,000 enrolled1 locationNCT01604395