RecruitingNCT06309979

A Study to Assess Growth in Children With Idiopathic Short Stature

A Multicenter, Observational Study to Characterize Growth in Children With Idiopathic Short Stature


Sponsor

BioMarin Pharmaceutical

Enrollment

300 participants

Start Date

Aug 8, 2024

Study Type

OBSERVATIONAL

Conditions

Summary

Study 111-903 will generate baseline growth data in children with ISS by collecting growth measurements and other variables of interest.


Eligibility

Min Age: 2 YearsMax Age: 16 Years

Inclusion Criteria5

  • Participants must be > 2 years old, and ≤ 14 years old (female) or ≤ 16 years old (males) at the time of signing the informed consent.
  • A height assessment corresponding to a height Z-score of ≤ -2.25 SDs in reference to the general population of the same age and sex, as calculated using the Centers for Disease Control and Prevention (CDC) growth chart (https://www.cdc.gov/growthcharts/zscore.htm).
  • Participants who have either never received hGH, or who are currently receiving hGH treatment.
  • Historic stimulation test result with serum or plasma GH level greater than 10 μg/L.
  • Parent(s) or guardian(s) are willing and able to provide written, signed informed consent.

Exclusion Criteria6

  • Diagnosis of systemic disease or condition that may cause short stature, eg renal, neoplastic, pulmonary, cardiac, gastrointestinal, immunologic and metabolic disease. Children with such diagnoses can be considered for inclusion if their condition is well controlled, at the discretion of the Medical Monitor.
  • Known presence of one or more pituitary hormone deficiencies
  • Bone age advanced over chronological age by more than 3 years.
  • For hGH naïve participants, historic stimulation test result with serum or plasma GH level greater than 10 μg/L or serum IGF-1 in the normal range for age (between -1.00 SDs and +2.00 SDs).
  • For participants currently on hGH treatment, historic results before GH treatment of stimulation test with serum or plasma GH level greater than 10 μg/L or serum IGF-1 test between -1.00 SDs and +2.00 SDs.
  • Have received an investigational product (IP) or investigational medical device for any purpose within 6 months before the Screening visit. .

Interested in this trial?

Get notified about updates and connect with the research team.


Locations(40)

Phoenix Children's Hospital - Thomas Campus (Main)

Phoenix, Arizona, United States

Children's Hospital Los Angeles

Los Angeles, California, United States

Harbor-UCLA Medical Center - The Lundquist Institute (Los Angeles Biomedical Research Institute (LA BioMed)

Los Angeles, California, United States

Children's Hospital of Orange County Main Campus - Orange

Orange, California, United States

Center Of Excellence in Diabetes and Endocrinology

Sacramento, California, United States

Rady Children's Hospital - San Diego

San Diego, California, United States

University of California San Francisco (UCSF)

San Francisco, California, United States

Connecticut Children's Medical Center

Hartford, Connecticut, United States

Yale School of Medicine

New Haven, Connecticut, United States

Children's National Health System

Washington D.C., District of Columbia, United States

Nemours Children's Clinic

Jacksonville, Florida, United States

Nicklaus Children's Hospital

Miami, Florida, United States

Nemours Children's Health System - Corporate Headquarters

Pensacola, Florida, United States

Centricity Research

Columbus, Georgia, United States

St. Luke's Children's Endocrinology

Boise, Idaho, United States

Rocky Mountain Diabetes Center - Idaho Falls

Idaho Falls, Idaho, United States

Rocky Mountain Clinical Research - Idaho Falls

Idaho Falls, Idaho, United States

University of Louisville School Of Medicine - Norton Children's Hospital

Louisville, Kentucky, United States

Ochsner Health Center for Children - New Orleans

New Orleans, Louisiana, United States

University of Michigan

Ann Arbor, Michigan, United States

University of Minnesota Medical School - Masonic Children's Hospital - Pediatric Specialty Care Explorer Clinic

Minneapolis, Minnesota, United States

Dartmouth-Hitchcock Medical Center

Lebanon, New Hampshire, United States

University of Iowa Stead Family Children's Hospital

Princeton, New Jersey, United States

UBMD Pediatrics

Buffalo, New York, United States

ACGC Research, NYU Ambulatory Care Garden City

Garden City, New York, United States

New York University Grossman School of Medicine

New York, New York, United States

Icahn School of Medicine at Mount Sinai (ISMMS) - The Mount Sinai Hospital (MSH) - Pediatric Associates

New York, New York, United States

Montefiore Medical Center (MMC) - The Children's Hospital at Montefiore (CHAM)

The Bronx, New York, United States

WakeMed Children's - Pediatric Endocrinology - North Raleigh

Raleigh, North Carolina, United States

Cincinnati Children's Hospital Medical Center Burnet Campus

Cincinnati, Ohio, United States

Nationwide Children's Hospital

Columbus, Ohio, United States

Prisma Health Children's Hospital - Midlands

Columbia, South Carolina, United States

Vanderbilt University Medical Center

Nashville, Tennessee, United States

University of Texas Southwestern Medical Center

Dallas, Texas, United States

Cook Children's Endocrinology

Fort Worth, Texas, United States

Baylor College of Medicine

Houston, Texas, United States

Seattle Children's Hospital

Seattle, Washington, United States

Charleston Area Medical Center (CAMC) Health System

Charleston, West Virginia, United States

Charleston Area Medical Center (CAMC) Health System

Charleston, West Virginia, United States

Medical College of Wisconsin, Children's Hospital

Milwaukee, Wisconsin, United States

View Full Details on ClinicalTrials.gov

For the most up-to-date information, visit the official listing.

Visit

NCT06309979


Related Trials