Myasthenic Syndrome Clinical Trials

2 recruiting

Myasthenic Syndrome Trials at a Glance

7 actively recruiting trials for myasthenic syndrome are listed on ClinicalTrialsFinder across 6 cities in 12 countries. The largest study group is Not Applicable with 2 trials, with the heaviest enrollment activity in Milan, Oxford, and Marseille. Lead sponsors running myasthenic syndrome studies include argenx, Centre Hospitalier Universitaire de Liege, and Heinrich-Heine University, Duesseldorf.

Browse myasthenic syndrome trials by phase

Treatments under study

About Myasthenic Syndrome Clinical Trials

Looking for clinical trials for Myasthenic Syndrome? There are currently 2 studies actively recruiting participants. Clinical trials offer access to new treatments before they are widely available, and every approved therapy in use today was first tested through a clinical trial.

Below you can browse trials, sign up for alerts when new Myasthenic Syndrome trials open, and view eligibility criteria for each study. Each listing includes the study phase, locations, and enrollment details.

Frequently Asked Questions

Common questions about Myasthenic Syndrome clinical trials

A clinical trial is a carefully designed research study that tests new medical treatments, drugs, devices, or approaches in human volunteers. Every approved medication and treatment available today was proven safe and effective through clinical trials.

All clinical trials are reviewed and approved by Institutional Review Boards (IRBs) — independent committees that evaluate patient safety. Trials follow strict protocols, and your health is monitored closely throughout. You can withdraw at any time.

Not necessarily. Many trials compare the new treatment against the current standard of care, meaning all participants receive active treatment. When placebos are used, they are typically combined with standard treatment, not given alone. The trial description will always specify the design.

Under the Affordable Care Act, most private insurers are required to cover routine patient care costs during a clinical trial. The sponsor typically covers the investigational treatment itself. Medicare also covers routine costs for qualifying trials.

Yes. Participation is completely voluntary. You can withdraw at any time, for any reason, without it affecting your access to standard medical care.

Each trial has specific eligibility criteria — including age, diagnosis, disease stage, prior treatments, and general health. Browse the trials listed above and check their eligibility sections. You can also contact the trial site directly to discuss your situation.

Showing 17 of 7 trials

Recruiting

A Natural History Study in Participants With Congenital Myasthenic Syndromes (CMS) Due to Mutations in DOK7, MUSK, AGRN, or LRP4

Congenital Myasthenic Syndrome
argenx100 enrolled20 locationsNCT06078553
Recruiting
Phase 1

A Phase 1b Study to Investigate Safety and Tolerability of ARGX-119 in Adult Participants With DOK7-Congenital Myasthenic Syndromes (CMS)

Congenital Myasthenic SyndromeCMS
argenx16 enrolled9 locationsNCT06436742
Recruiting
Not Applicable

Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease

Myasthenia GravisAmyotrophic Lateral SclerosisNeuromuscular Diseases (NMD)+15 more
University of Missouri-Columbia50 enrolled1 locationNCT07478172
Recruiting

A Prospective Natural History and Outcome Measure Validation Study of Congenital Myasthenic Syndromes

Myasthenic Syndromes, Congenital
National Institute of Neurological Disorders and Stroke (NINDS)75 enrolled1 locationNCT06630650
Recruiting
Phase 1

Patients With Congenital Myasthenic Syndrome Will be Treated With Mesenchymal Stem Cell Exosome Solution

Congenital Myasthenic Syndrome
The Foundation for Orthopaedics and Regenerative Medicine20 enrolled3 locationsNCT07226726
Recruiting
Not Applicable

Gait Analysis Parameter and Upper Limb Evaluation in Adult Patients With Neurological or Metabolic Pathology

Myasthenia GravisHuntington DiseaseNeuromuscular Diseases+9 more
Centre Hospitalier Universitaire de Liege300 enrolled1 locationNCT07136844
Recruiting

Patient Observation With Environmental and Wearable Sensors in Myasthenia Gravis

Myasthenia GravisMyasthenic Syndrome
Heinrich-Heine University, Duesseldorf20 enrolled1 locationNCT06441825