Phase 2 Noonan Syndrome Clinical Trials
2 recruitingPhase 2
What is a Phase 2 trial?
Phase 2 trials evaluate whether a treatment works for a specific condition and further assess its safety. These studies typically enroll several hundred participants and provide preliminary data on effectiveness.
Showing 1–2 of 2 trials
Recruiting
Phase 2
A Basket Study of Vosoritide in Children With Turner Syndrome, Short Stature Homeobox-Containing Gene Deficiency, and Noonan Syndrome With Inadequate Growth During or After Human Growth Hormone Treatment
Noonan SyndromeTurner SyndromeShort Stature Homeobox- Containing Gene SHOX Deficiency
BioMarin Pharmaceutical54 enrolled24 locationsNCT06668805
Recruiting
Phase 2
MEK Inhibitors for the Treatment of Hypertrophic Cardiomyopathy in Patients With RASopathies
Noonan SyndromeCardiomegaly
Medical University of Warsaw40 enrolled1 locationNCT06555237