Pelizaeus-Merzbacher Disease Clinical Trials in Le Kremlin-Bicêtre
2 recruitingLe Kremlin-Bicêtre, France
Showing 1–2 of 2 trials
Recruiting
Rocket Study: A Study to Characterize Biomarkers and Disease Progression in Participants With Pelizaeus-Merzbacher Disease
Pelizaeus-Merzbacher Disease
Ionis Pharmaceuticals, Inc.32 enrolled9 locationsNCT05659901
Recruiting
Phase 1
Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD)
Pelizaeus-Merzbacher Disease
Ionis Pharmaceuticals, Inc.24 enrolled7 locationsNCT06150716