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Phelan-McDermid Syndrome
Boston, Massachusetts
Phelan-McDermid Syndrome Clinical Trials in Boston, Massachusetts
1 recruiting
Boston, Massachusetts
Showing
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1
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Recruiting
Phase 1
Phase 2
JAG201 Gene Therapy Study in Children & Adults With SHANK3 Haploinsufficiency
Phelan-McDermid Syndrome
SHANK3 Haploinsufficiency
Jaguar Gene Therapy, LLC
6 enrolled
3 locations
NCT06662188
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