Phase 2 Phenylketonuria Clinical Trials
4 recruitingPhase 2
What is a Phase 2 trial?
Phase 2 trials evaluate whether a treatment works for a specific condition and further assess its safety. These studies typically enroll several hundred participants and provide preliminary data on effectiveness.
Showing 1–4 of 4 trials
Recruiting
Phase 2
A Phase 2 Study of JNT-517 in Adolescent Participants With Phenylketonuria
Phenylketonuria (PKU)
Otsuka Pharmaceutical Development & Commercialization, Inc.10 enrolled7 locationsNCT06637514
Recruiting
Phase 1Phase 2
AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)
Phenylketonurias
NGGT INC.12 enrolled5 locationsNCT06332807
Recruiting
Phase 1Phase 2
Safety and Efficacy Study of NGGT002 in cPKU Adult Subjects
Phenylketonurias
NGGT (Suzhou) Biotechnology Co., Ltd.18 enrolled2 locationsNCT06687733
Completed
Phase 2
A Phase 2, Randomized, Double Crossover, Open-Label, Active-Controlled Proof-of-Concept Study of CNSA-001 in Phenylketonuria Patients
Phenylketonuria
Censa Pharmaceuticals Australia Pty Ltd30 enrolled4 locationsACTRN12618001031257