Pompe Disease Clinical Trials in Irvine, California
4 recruitingIrvine, California
Showing 1–4 of 4 trials
Recruiting
Phase 2
Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
Pompe Disease
Shionogi45 enrolled28 locationsNCT07123155
Recruiting
Pompe Disease Registry Protocol
Pompe DiseaseGlycogen Storage Disease Type II
Genzyme, a Sanofi Company2,000 enrolled272 locationsNCT00231400
Recruiting
Phase 1Phase 2
A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late Onset Pompe Disease (PROGRESS-GT LOPD)
Pompe Disease (Late-onset)
AskBio Inc12 enrolled10 locationsNCT07282847
Recruiting
A Global Prospective Observational Registry of Patients With Pompe Disease
Pompe Disease
Amicus Therapeutics500 enrolled41 locationsNCT06121011