Phase 1 Prion Disease Clinical Trials

2 recruitingPhase 1

What is a Phase 1 trial?

Phase 1 trials test a new treatment in a small group of people for the first time. The primary goal is to evaluate safety, determine a safe dosage range, and identify side effects. These studies typically enroll 20 to 80 participants.

Showing 1–2 of 2 trials

Recruiting

Phase 1Phase 2

PrProfile: A Study to Assess the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of ION717

Prion Disease

Ionis Pharmaceuticals, Inc.76 enrolled13 locationsNCT06153966

Recruiting

Phase 1

PrP-targeting siRNA Safety & Mechanism Study

Prion Disease

Broad Institute of MIT and Harvard30 enrolled3 locationsNCT07444580