Phase 1 Propionic Acidemia Clinical Trials

3 recruitingPhase 1

What is a Phase 1 trial?

Phase 1 trials test a new treatment in a small group of people for the first time. The primary goal is to evaluate safety, determine a safe dosage range, and identify side effects. These studies typically enroll 20 to 80 participants.

Showing 1–3 of 3 trials

Recruiting

Phase 1

AAVrh10-PCCA Gene Therapy for Propionic Acidemia

Propionic Acidemia

Mayo Clinic9 enrolled1 locationNCT07643844

Recruiting

Phase 1Phase 2

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

Propionic Acidemia

ModernaTX, Inc.50 enrolled22 locationsNCT05130437

Recruiting

Phase 1Phase 2

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

Propionic Acidemia

ModernaTX, Inc.77 enrolled35 locationsNCT04159103