Phase 3 Rett Syndrome Clinical Trials
3 recruitingPhase 3
What is a Phase 3 trial?
Phase 3 trials compare the new treatment against the current standard of care in large groups, often hundreds to thousands of participants. Successful Phase 3 results are typically required for regulatory approval.
Showing 1–3 of 3 trials
Recruiting
Phase 3
To Investigate the Efficacy of Treatment With Oral NA-921 (Bionetide) Versus Placebo in Females With Rett Syndrome
Rett Syndrome
Biomed Industries, Inc.210 enrolled18 locationsNCT06840496
Recruiting
Phase 3
A Novel, Regulated Gene Therapy (NGN-401) Study for Females With Rett Syndrome
Rett Syndrome
Neurogene Inc.33 enrolled16 locationsNCT05898620
Recruiting
Phase 3
A Phase 1/2/3 Study of TSHA-102 Gene Therapy in Females With Rett Syndrome (REVEAL Pivotal Study)
Rett Syndrome
Taysha Gene Therapies, Inc.15 enrolled6 locationsNCT05606614