Short Stature Clinical Trials

1 recruiting

Short Stature Trials at a Glance

10 actively recruiting trials for short stature are listed on ClinicalTrialsFinder across 6 cities in 8 countries. The largest study group is Phase 2 with 4 trials, with the heaviest enrollment activity in Washington D.C., Miami, and Boise. Lead sponsors running short stature studies include BioMarin Pharmaceutical, Changchun GeneScience Pharmaceutical Co., Ltd., and Ascendis Pharma A/S.

Browse short stature trials by phase

Treatments under study

About Short Stature Clinical Trials

Looking for clinical trials for Short Stature? There are currently 1 studies actively recruiting participants. Clinical trials offer access to new treatments before they are widely available, and every approved therapy in use today was first tested through a clinical trial.

Below you can browse trials, sign up for alerts when new Short Stature trials open, and view eligibility criteria for each study. Each listing includes the study phase, locations, and enrollment details.

Frequently Asked Questions

Common questions about Short Stature clinical trials

A clinical trial is a carefully designed research study that tests new medical treatments, drugs, devices, or approaches in human volunteers. Every approved medication and treatment available today was proven safe and effective through clinical trials.

All clinical trials are reviewed and approved by Institutional Review Boards (IRBs) — independent committees that evaluate patient safety. Trials follow strict protocols, and your health is monitored closely throughout. You can withdraw at any time.

Not necessarily. Many trials compare the new treatment against the current standard of care, meaning all participants receive active treatment. When placebos are used, they are typically combined with standard treatment, not given alone. The trial description will always specify the design.

Under the Affordable Care Act, most private insurers are required to cover routine patient care costs during a clinical trial. The sponsor typically covers the investigational treatment itself. Medicare also covers routine costs for qualifying trials.

Yes. Participation is completely voluntary. You can withdraw at any time, for any reason, without it affecting your access to standard medical care.

Each trial has specific eligibility criteria — including age, diagnosis, disease stage, prior treatments, and general health. Browse the trials listed above and check their eligibility sections. You can also contact the trial site directly to discuss your situation.

Showing 110 of 10 trials

Recruiting
Phase 3

Trial Investigating the Efficacy and Safety of Weekly Lonapegsomatropin Compared to Daily Somatropin in Children and Adolescents With Short Stature or Growth Failure Due to Growth Hormone Sufficient Disorders

Turner SyndromeIdiopathic Short StatureShort Stature Homeobox Gene Mutation+1 more
Ascendis Pharma A/S186 enrolled11 locationsNCT07221851
Recruiting
Phase 2

A Phase 2 Study of Vosoritide in Children With Idiopathic Short Stature

Idiopathic Short Stature
BioMarin Pharmaceutical100 enrolled47 locationsNCT06382155
Recruiting
Phase 3

The Efficacy and Safety of Inpegsomatropin Injection in Children With Idiopathic Short Stature

Idiopathic Short Stature
Xiamen Amoytop Biotech Co., Ltd.300 enrolled38 locationsNCT06927310
Recruiting
Phase 2

A Basket Study of Vosoritide in Children With Turner Syndrome, Short Stature Homeobox-Containing Gene Deficiency, and Noonan Syndrome With Inadequate Growth During or After Human Growth Hormone Treatment

Noonan SyndromeTurner SyndromeShort Stature Homeobox- Containing Gene SHOX Deficiency
BioMarin Pharmaceutical54 enrolled24 locationsNCT06668805
Recruiting
Phase 2

A Phase II Study of PEG-rhGH Injection for Short Children Born Small for Gestational Age: Efficacy, Safety, and Pharmacokinetics

Short Stature Children Born Small for Gestational Age (SGA)
Changchun GeneScience Pharmaceutical Co., Ltd.72 enrolled1 locationNCT07260500
Recruiting

A Study to Assess Growth in Children With Idiopathic Short Stature

Idiopathic Short Stature
BioMarin Pharmaceutical300 enrolled40 locationsNCT06309979
Recruiting

Long-term Efficacy and Safety Evaluation of Growth Hormone in Children in China(CGLS)

Childhood Short Stature
Xiaoping Luo10,000 enrolled1 locationNCT06110910
Recruiting
Phase 2

Vosoritide for Short Stature in Turner Syndrome

Turner SyndromeShort Stature
Roopa Kanakatti Shankar, MBBS, MS20 enrolled1 locationNCT05849389
Recruiting

Long-term Safety and Effectiveness of Growtropin®-II Treatment in Children With Short Stature

Turner SyndromeGrowth Hormone DeficiencySmall for Gestational Age+1 more
Dong-A ST Co., Ltd.2,500 enrolled1 locationNCT04798690
Recruiting

Long-term Safety and Effectiveness of Growth Hormone With GHD, TS, CRF, SGA , ISS and PWS in Children

Turner SyndromeChronic Renal FailureGrowth Hormone Deficiency+2 more
LG Chem6,000 enrolled1 locationNCT01604395