Phase 3 Spinal Muscular Atrophy (SMA) Clinical Trials

2 recruitingPhase 3

What is a Phase 3 trial?

Phase 3 trials compare the new treatment against the current standard of care in large groups, often hundreds to thousands of participants. Successful Phase 3 results are typically required for regulatory approval.

Showing 1–2 of 2 trials

Recruiting

Phase 3

Long-term Follow-up of Patients With Spinal Muscular Atrophy Treated With OAV101 in Clinical Trials

Spinal Muscular Atrophy (SMA)

Novartis Pharmaceuticals175 enrolled32 locationsNCT05335876

Recruiting

Phase 3

Real World Clinical Effectiveness & Safety of Vesemnogene Lantuparvovec for Spinal Muscular Atrophy (SMA) in Low-middle Income Countries (LMIC).

Spinal Muscular Atrophy (SMA)

Lantu Biopharma15 enrolled1 locationNCT07265232