Phase 2 Spinal Muscular Atrophy Type 3 Clinical Trials

2 recruitingPhase 2

What is a Phase 2 trial?

Phase 2 trials evaluate whether a treatment works for a specific condition and further assess its safety. These studies typically enroll several hundred participants and provide preliminary data on effectiveness.

Showing 1–2 of 2 trials

Recruiting

Phase 2

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

Spinal Muscular AtrophySMASpinal Muscular Atrophy Type 3+3 more

Scholar Rock, Inc.52 enrolled25 locationsNCT07047144

Recruiting

Phase 1Phase 2

Evaluation of Safety and Efficacy of Gene Therapy Drug in the Treatment of Spinal Muscular Atrophy (SMA) Type 3 Patients

Spinal Muscular Atrophy Type 3

GeneCradle Inc21 enrolled1 locationNCT06421831