Phase 1 Stargardt Disease 1 Clinical Trials

2 recruitingPhase 1

What is a Phase 1 trial?

Phase 1 trials test a new treatment in a small group of people for the first time. The primary goal is to evaluate safety, determine a safe dosage range, and identify side effects. These studies typically enroll 20 to 80 participants.

Showing 1–2 of 2 trials

Recruiting

Phase 1Phase 2

Safety and Preliminary Efficacy of VG801 in Patients With ABCA4 Mutation-associated Retinal Dystrophy (Stargardt Disease)

Retinal Dystrophy Due to Biallelic ABCA4 MutationsStargardt Disease 1

VeonGen Therapeutics GmbH15 enrolled1 locationNCT07002398

Recruiting

Phase 1Phase 2

Study to Evaluate ACDN-01 in ABCA4-related Stargardt Retinopathy (STELLAR)

Stargardt DiseaseStargardt Disease 1Cone-Rod Dystrophy+1 more

Ascidian Therapeutics, Inc15 enrolled10 locationsNCT06467344