RecruitingPhase 3NCT03633708

A Trial of Etelcalcetide in Pediatric Participants With Secondary Hyperparathyroidism and Chronic Kidney Disease on Hemodialysis

Phase 3, Randomized, Open-label, Controlled, Multiple Dose, Efficacy, Safety, Pharmacokinetic, and Pharmacodynamic Study of Etelcalcetide in Pediatric Subjects 28 Days to < 18 Years of Age With Secondary Hyperparathyroidism and Chronic Kidney Disease Receiving Maintenance Hemodialysis


Sponsor

Amgen

Enrollment

56 participants

Start Date

Apr 29, 2019

Study Type

INTERVENTIONAL

Conditions

Summary

This is a phase 3 trial of etelcalcetide in pediatric participants with secondary hyperparathyroidism (SHPT) and chronic kidney disease (CKD) on hemodialysis.


Eligibility

Min Age: 0 YearsMax Age: 18 Years

Plain Language Summary

Simplified for easier understanding

This trial is testing a drug called etelcalcetide in children on hemodialysis (kidney dialysis) who have a condition called secondary hyperparathyroidism — where the parathyroid glands become overactive because of chronic kidney disease, causing dangerously high hormone levels that can weaken bones. **You may be eligible if...** - Your child is between 28 days and 17 years old and weighs at least 7 kg - They have chronic kidney disease and are on hemodialysis - They have been diagnosed with secondary hyperparathyroidism with very high parathyroid hormone (PTH) levels (above 300 pg/mL on two separate tests) - Their calcium levels are within acceptable ranges for their age **You may NOT be eligible if...** - Your child is not on hemodialysis - Their calcium levels are too low - They have had a severe reaction to etelcalcetide or similar drugs before - They are pregnant Talk to your doctor to see if this trial is right for you.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

DRUGEtelcalcetide

Etelcalcetide has been shown to be safe and efficacious in treating adult CKD patients with SHPT by simultaneously controlling iPTH, Ca, and phosphorus and has recently been approved for use in adult patients with SHPT treated with hemodialysis in both the United States and Europe

OTHERStandard of Care

Standard of care, which can include therapy with vitamin D sterols, Ca supplementation, and/or phosphate binders


Locations(43)

Childrens Hospital of Los Angeles

Los Angeles, California, United States

Childrens Hospital Colorado

Aurora, Colorado, United States

Childrens Mercy Hospital

Kansas City, Missouri, United States

Mount Sinai Kidney Center - B1 Renal Treatment

New York, New York, United States

Cincinnati Childrens Hospital Medical Center

Cincinnati, Ohio, United States

Cleveland Clinic Foundation

Cleveland, Ohio, United States

The Childrens Hospital at Oklahoma University Medical Center

Oklahoma City, Oklahoma, United States

Childrens Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Childrens Medical Center Dallas

Dallas, Texas, United States

Primary Childrens Hospital Outpatient Services

Salt Lake City, Utah, United States

Fresenius Escobar

Belen de Escobar, Buenos Aires, Argentina

Hospital Italiano

Cuidad Autonoma de Buenos Aires, Buenos Aires, Argentina

Centro Infantil Del Rinon

San Miguel de Tucumán, Tucumán Province, Argentina

Manipal Hospital

Bangalore, Karnataka, India

KLES Dr Prabhakar Kore Hospital and Medical Research Centre

Belagavi, Karnataka, India

Fortis Flt Lt Rajan Dhall Hospital

New Delhi, National Capital Territory of Delhi, India

All India Institute of Medical Sciences

New Delhi, National Capital Territory of Delhi, India

Sir Ganga Ram Hospital

New Delhi, National Capital Territory of Delhi, India

NRS Medical College and Hospital

Kolkata, West Bengal, India

Hospital Raja Perempuan Zainab II

Kota Bharu, Kelantan, Malaysia

Hospital Wanita Dan Kanak-Kanak Kuala Lumpur

Kuala Lumpur, Kuala Lumpur, Malaysia

Hospital TuanKu Jaafar

Seremban, Negeri Sembilan, Malaysia

SBHI Pediatrics city clinical hospital of Saint Vladimir

Moscow, Russia

SBHI Children's City Multidisciplinary Clinical Specialized Center of High Medical Technologies

Saint Petersburg, Russia

State Budgetary Healthcare Institution Samara Regional Clinical Hospital na V D Seredavin

Samara, Russia

National University Hospital

Singapore, Singapore

Asan Medical Center

Seoul, South Korea

Seoul National University Hospital

Seoul, South Korea

Pusan National University Yangsan Hospital

Yangsan-si, Gyeongsangnam-do, South Korea

Kaohsiung Veterans General Hospital

Kaohsiung City, Taiwan

National Cheng Kung University Hospital

Tainan, Taiwan

National Taiwan University Hospital

Taipei, Taiwan

Linkou Chang Gung Memorial Hospital

Taoyuan, Taiwan

Hacettepe Universitesi Tip Fakultesi Hastanesi

Ankara, Turkey (Türkiye)

Baskent Universitesi Ankara Hastanesi

Ankara, Turkey (Türkiye)

Gazi Universitesi Saglik Arastirma ve Uygulama Merkezi Gazi Hastanesi

Ankara, Turkey (Türkiye)

Ankara Bilkent Sehir Hastanesi

Ankara, Turkey (Türkiye)

Firat Universitesi Tip Fakultesi Hastanesi

Elâzığ, Turkey (Türkiye)

Istanbul Universitesi Cerrahpasa Tip Fakultesi

Istanbul, Turkey (Türkiye)

Marmara Universitesi Tip Fakultesi Hastanesi

Istanbul, Turkey (Türkiye)

Ege Universitesi Tip Fakultesi Hastanesi

Izmir, Turkey (Türkiye)

Erciyes Universitesi Tip Fakultesi Hastanesi

Kayseri, Turkey (Türkiye)

National Childrens Specializated Hospital Okhmadit

Kyiv, Ukraine

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NCT03633708


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