RecruitingNCT04202341

Registry of Participants With Generalized Myasthenia Gravis Treated With Alexion C5 Inhibition Therapies (C5ITs)

Long-Term, Observational, Global Registry of Patients With Generalized Myasthenia Gravis Who Have Received Treatment With Complement C5 Inhibition Therapies (C5ITs)


Sponsor

Alexion Pharmaceuticals, Inc.

Enrollment

500 participants

Start Date

Dec 2, 2019

Study Type

OBSERVATIONAL

Conditions

Summary

Long-term, multicenter, multinational, observational, registry of patients with gMG that is designed to collect data on clinical outcomes and safety in patients prescribed Alexion C5 inhibitor therapies (C5IT) such as eculizumab (Soliris®) and ravulizumab (Ultomiris®).


Eligibility

Min Age: 18 Years

Inclusion Criteria3

  • Participants with a diagnosis of gMG who are treated with Alexion C5IT at the time of enrollment, including patients previously treated with Soliris or Ultomiris and withdrawn from treatment.
  • Capable of giving signed informed consent, which includes compliance with the protocol requirements and restrictions.
  • Participants must have myasthenia gravis historical data, such as MG-ADL and MGFA class, available to be enrolled in the Registry.

Exclusion Criteria1

  • \. Participants currently enrolled in an Alexion-sponsored interventional clinical study for treatment of gMG cannot be enrolled in the Alexion gMG Registry while enrolled/participating in the clinical study for gMG therapy.

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Locations(51)

Clinical Trial Site

Birmingham, Alabama, United States

Clinical Trial Site

Scottsdale, Arizona, United States

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Fresno, California, United States

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Orange, California, United States

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Rancho Mirage, California, United States

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Sylmar, California, United States

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Colorado Springs, Colorado, United States

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Fort Collins, Colorado, United States

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New Haven, Connecticut, United States

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Washington D.C., District of Columbia, United States

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Clearwater, Florida, United States

Clincal Trial Site

Gainesville, Florida, United States

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Jacksonville, Florida, United States

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Tampa, Florida, United States

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Augusta, Georgia, United States

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Iowa City, Iowa, United States

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Lexington, Kentucky, United States

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Boston, Massachusetts, United States

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Lansing, Michigan, United States

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Columbia, Missouri, United States

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New Hyde Park, New York, United States

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Chapel Hill, North Carolina, United States

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Charlotte, North Carolina, United States

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Durham, North Carolina, United States

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Dayton, Ohio, United States

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Philadelphia, Pennsylvania, United States

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Chattanooga, Tennessee, United States

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Knoxville, Tennessee, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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Burlington, Vermont, United States

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Milwaukee, Wisconsin, United States

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Vienna, Austria

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Brampton, Ontario, Canada

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London, Ontario, Canada

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Montreal, Quebec, Canada

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Chengdu, Sichuan, China

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Beijing, China

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Changchun, China

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Chengdu, China

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Guangzhou, China

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Jinan, China

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Nanchang, China

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Qingdao, China

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Shijiazhuang, China

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Hanover, Hannover, Germany

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Milan, Italy

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Naples, Italy

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Abhā, Saudi Arabia

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Jeddah, Saudi Arabia

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Riyadh, Saudi Arabia

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