RecruitingPhase 2Phase 3NCT04256317

A Multi-phase Study of ASTX030 (Azacitidine and Cedazuridine) in Myeloid Neoplasm Alone or in Combination With Venetoclax in AML (AZTOUND Study)

A Multi-phase, Pharmacokinetics, Safety, and Efficacy Study of ASTX030 (Azacitidine and Cedazuridine) as Monotherapy in Subjects With Myeloid Neoplasm or in Combination With Venetoclax in Subjects With AML (AZTOUND Study)


Sponsor

Taiho Oncology, Inc.

Enrollment

316 participants

Start Date

May 21, 2020

Study Type

INTERVENTIONAL

Conditions

Summary

Study ASTX030-01 is a multi-phase study comprising of Phases 1-3 Monotherapy arms, and Phase 1 and Phase 2 Combination Therapy arms. Phase 1 Monotherapy consists of an open-label Dose Escalation Stage (Stage A) using multiple cohorts at escalating dose levels of oral cedazuridine and azacitidine (only one study drug will be escalated at a time) followed by a Dose Expansion Stage (Stage B). Phase 2 Monotherapy is a randomized, open-label, crossover study to compare oral ASTX030 to subcutaneous (SC) azacitidine. Phase 3 Monotherapy is a randomized open-label crossover study comparing the final fixed dose of oral ASTX030 to SC azacitidine. Phase 1 Combination Therapy is an open-label, multicenter, randomized, exploratory study comparing ASTX030 and SC azacitidine in combination with venetoclax in participants with treatment-naïve AML. Phase 2 Combination Therapy is an open-label, single arm, study evaluating the efficacy, safety, pharmacokinetics (PK), and drug interactions of ASTX030 in combination with venetoclax in participants with treatment-naïve AML. The duration of this multi-phase study is approximately 8 years.


Eligibility

Min Age: 18 Years

Plain Language Summary

Simplified for easier understanding

This study is testing an oral (pill) form of a drug called azacitidine, combined with another drug cedazuridine, for patients with certain blood/bone marrow diseases. It is also testing combining this pill with venetoclax for leukemia patients, to see if the pills work as well as injections. **You may be eligible if:** - You have myelodysplastic syndrome (MDS), chronic myelomonocytic leukemia (CMML), or acute myeloid leukemia (AML) - You are a candidate to receive azacitidine as part of your treatment - You meet age and health requirements set by the study team **You may NOT be eligible if:** - You have significant organ dysfunction (especially kidneys or liver) - You are pregnant or not using appropriate contraception - You have other active cancers or serious health conditions preventing participation Talk to your doctor to see if this trial is right for you.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

DRUGAzacitidine

Tablets/Capsules for oral administration and powder for reconstitution to aqueous suspension for SC administration.

DRUGASTX030 (cedazuridine + azacitidine)

FDC Capsules for oral administration.

DRUGAzacitidine

Powder for reconstitution to aqueous suspension for SC administration.

DRUGASTX030 (cedazuridine + azacitidine)

Tablets/Capsules for oral administration.

DRUGCedazuridine

Tablets for oral administration.

DRUGVenetoclax

Oral tablets.


Locations(71)

Keck School of Medicine of USC

Los Angeles, California, United States

UC Irvine Health - Chao Family Comprehensive Cancer Center

Orange, California, United States

Yale University

New Haven, Connecticut, United States

University of Miami - Sylvester Comprehensive Cancer Center

Miami, Florida, United States

University of Emory - Winship Cancer Institute

Atlanta, Georgia, United States

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

John Theurer Cancer Center / Hackensack University

Hackensack, New Jersey, United States

Roswell Park Comprehensive Cancer Center

Buffalo, New York, United States

New York University Langone Hospital - Long Island

Mineola, New York, United States

Perlmutter Cancer Center - 34th Street

New York, New York, United States

Icahn School of Medicine at Mount Sinai

New York, New York, United States

Weill Cornell Medical Center

New York, New York, United States

Montefiore Medical Center

The Bronx, New York, United States

Duke University

Durham, North Carolina, United States

Ohio State University Comprehensive Cancer Center (OSUCCC) - The James Cancer Hospital and Solove Research Institute

Columbus, Ohio, United States

Oregon Health and Science University

Portland, Oregon, United States

Oregon Oncology Specialists

Salem, Oregon, United States

Hollings Cancer Center

Charleston, South Carolina, United States

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Baylor Research Institute dba Baylor Scott & White Research Institute

Dallas, Texas, United States

University of Texas Southwestern Medical Center

Dallas, Texas, United States

MD Anderson Cancer Center

Houston, Texas, United States

Seattle Cancer Care Alliance

Seattle, Washington, United States

Froedtert & Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Eastern Health - Health Sciences Centre

St. John's, Newfoundland and Labrador, Canada

Princess Margaret Cancer Centre

Toronto, Ontario, Canada

Fakultni Nemocnice Ostrava

Ostrava, Moravian-Silesian, Czechia

Fakultní Nemocnice Královské Vinohrady

Prague, Prague, Czechia

Vseobecna Fakultni Nemocnice v Praze

Prague, Prague, Czechia

Institut Universitaire du Cancer de Toulouse (IUCT) Oncopole

Toulouse, Haute-Garonne, France

Hôpital l'Archet

Nice, Provence-Alpes-Côte d'Azur Region, France

Hôpital Saint-Louis

Paris, Île-de-France Region, France

Universitätsklinikum Freiburg

Freiburg im Breisgau, Baden-Wurttemberg, Germany

Universitätsklinikum Heidelberg

Heidelberg, Baden-Wurttemberg, Germany

Städtisches Klinikum Braunschweig

Braunschweig, Lower Saxony, Germany

Universitätsklinikum Halle

Halle, Saxony-Anhalt, Germany

Szent-Györgyi Albert Klinikai Központ, II. sz. Belgyógyászati Klinika és Kardiológiai Központ

Szeged, Csongrád megye, Hungary

Petz Aladár Győr-Moson-Sopron Vármegyei Egyetemi Oktató Kórház

Győr, Győr-Moson-Sopron, Hungary

Debreceni Egyetem Klinikai Központ

Debrecen, Hajdú-Bihar, Hungary

Semmelweis Egyetem Belgyógyászati és Hematológiai Klinika

Budapest, Hungary

Ospedale Santa Maria delle Croci di Ravenna

Ravenna, Emilia-Romagna, Italy

Azienda Ospedaliero - Universitaria Careggi

Florence, Florence, Italy

Azienda Ospedaliera Ordine Mauriziano di Torino

Torino, Turin, Italy

Azienda Ospedaliero-Universitaria di Bologna - Policlinico Sant Orsola-Malpighi

Bologna, Italy

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

Milan, Italy

Azienda Ospedaliero-Universitaria Maggiore della Carità di Novara

Novara, Italy

Fondazione PTV - Policlinico Tor Vergata

Roma, Italy

Umberto I - Policlinico di Roma

Roma, Italy

Azienda Ospedaliero-Universitaria Citta della Salute e della Scienza di Torino

Torino, Italy

Samodzielny Publiczny Szpital Kliniczny nr 1 w Lublinie

Lublin, Lublin Voivodeship, Poland

Wojewódzkie Wielospecjalistyczne Centrum

Lodz, Lódzkie, Poland

Szpitale Pomorskie Spółka Z Ograniczoną Odpowiedzialnością

Gdynia, Pomeranian Voivodeship, Poland

Institut Català d'Oncologia Badalona

Badalona, Barcelona, Spain

Institut Català d'Oncologia - Hospital Duran i Reynals (ICO L'Hospitalet)

L'Hospitalet de Llobregat, Barcelona, Spain

Clinica Universidad de Navarra - Pamplona

Pamplona, Navarre, Spain

Hospital Universitario Central de Asturias

Oviedo, Principality of Asturias, Spain

Hospital Universitari Vall d'Hebrón

Barcelona, Spain

Hospital Clinic de Barcelona

Barcelona, Spain

Hospital San Pedro de Alcantara

Cáceres, Spain

Institut Català d'Oncologia Girona (ICO Girona)

Girona, Spain

Hospital Universitario Virgen de las Nieves

Granada, Spain

Hospital General Universitario Gregorio Marañón

Madrid, Spain

Clínica Universidad de Navarra - Madrid

Madrid, Spain

MD Anderson Cancer Center Madrid

Madrid, Spain

Hospital Universitario La Paz

Madrid, Spain

Hospital Quirónsalud Málaga

Málaga, Spain

Complejo Asistencial Universitario de Salamanca - Hospital Clínico

Salamanca, Spain

Hospital Universitari i Politècnic La Fe

Valencia, Spain

King's College Hospital NHS Foundation Trust

London, England, United Kingdom

The Christie NHS Foundation Trust

Manchester, England, United Kingdom

University Hospital Southampton NHS Foundation Trust

Southampton, England, United Kingdom

View Full Details on ClinicalTrials.gov

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NCT04256317


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