RecruitingPhase 3NCT04528082

Apremilast Pediatric Study in Children With Active Oral Ulcers Associated With Behçet's Disease

A Phase 3, Multicenter, Double-blind, Randomized, Placebo-controlled, Parallel Group Study, Followed by an Active Treatment Phase to Evaluate the Efficacy and Safety of Apremilast in Children From 2 to Less Than 18 Years of Age With Active Oral Ulcers Associated With Behçet's Disease (BEAN)


Sponsor

Amgen

Enrollment

60 participants

Start Date

Sep 9, 2021

Study Type

INTERVENTIONAL

Conditions

Summary

The aim of this study is to estimate the efficacy of apremilast compared to placebo in the treatment of oral ulcers in pediatric participants from 2 to \< 18 years of age with oral ulcers associated with Behçet's disease (BD) through week 12.


Eligibility

Min Age: 2 YearsMax Age: 17 Years

Inclusion Criteria5

  • Male or Female participants 2 to < 18 years of age at randomization.
  • Diagnosed with BD meeting the ISGBD criteria at any time prior to the screening visit.
  • Oral ulcers that occurred ≥ 3 times within the 12-month period prior to the screening visit.
  • Participant must have ≥ 2 oral ulcers at both the screening visit and on day 1.
  • Participant has had prior treatment with ≥ 1 non-biologic BD therapy, such as, but not limited to, topical corticosteroids or systemic treatment.

Exclusion Criteria5

  • Behçet's disease-related active major organ involvement - pulmonary (eg, pulmonary artery aneurysm), vascular (eg, thrombophlebitis), gastrointestinal (eg, ulcers along the gastrointestinal tract), or CNS (eg, meningoencephalitis) manifestations, or ocular lesions (eg, uveitis) requiring immunosuppressive therapy; however:
  • Previous major organ involvement is allowed if it occurred ≥1 year prior to the screening visit and is not active at time of enrollment
  • Participants with mild BD-related ocular lesions not requiring systemic immunosuppressive therapy are allowed
  • Participants with BD-related arthritis and BD-skin manifestations are also allowed.
  • Previous exposure to biologic therapies for the treatment of BD oral ulcers, previous biologic exposure is allowed for other indications (including other manifestations of BD).

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Interventions

DRUGApremilast

Participants will receive apremilast orally.

DRUGPlacebo

Participants will receive the matching placebo orally.


Locations(27)

Hospices Civils de Lyon Hopital Femme Mere Enfant

Bron, France

Hopital Necker Enfants Malades

Paris, France

Hopital Robert Debre

Paris, France

Agia Sofia Children Hospital

Athens, Greece

Attikon University General Hospital

Athens, Greece

General Hospital of Thessaloniki Ippokrateio

Thessaloniki, Greece

Meir Medical Center

Kfar Saba, Israel

Ospedale Santissima Annunziata

Chieti, Italy

IRCCS Istituto Giannina Gaslini

Genova, Italy

Azienda Socio Sanitaria Territoriale Centro Specialistico Ortopedico Traumatologico Gaetano Pini

Milan, Italy

IRCCS Ospedale Pediatrico Bambino Gesu

Roma, Italy

Hospital Universitario Virgen del Rocio

Seville, Andalusia, Spain

Hospital Universitari Vall d Hebron

Barcelona, Catalonia, Spain

Hospital Sant Joan de Deu

Esplugues de Llobregat, Catalonia, Spain

Hospital Universitari i Politecnic La Fe

Valencia, Valencia, Spain

Hospital Universitario Ramon y Cajal

Madrid, Spain

Hospital Universitario La Paz

Madrid, Spain

Centre Hospitalier Universitaire Vaudois

Lausanne, Switzerland

Hacettepe Universitesi Tip Fakultesi Hastanesi

Ankara, Turkey (Türkiye)

Istanbul Universitesi Istanbul Tip Fakultesi Hastanesi

Istanbul, Turkey (Türkiye)

Istanbul Universitesi Cerrahpasa Tip Fakultesi

Istanbul, Turkey (Türkiye)

Umraniye Egitim ve Arastirma Hastanesi

Istanbul, Turkey (Türkiye)

Dokuz Eylul Universitesi Tip Fakultesi Hastanesi

Izmir, Turkey (Türkiye)

Erciyes Universitesi Tip Fakultesi Hastanesi

Kayseri, Turkey (Türkiye)

Birmingham Childrens Hospital

Birmingham, United Kingdom

Alder Hey Childrens Hospital

Liverpool, United Kingdom

John Radcliffe Hospital

Oxford, United Kingdom

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NCT04528082


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