RecruitingNCT04561518

ConTTRibute: A Global Observational Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis)

ConTTRibute: A Global Observational Multicenter Long-Term Study of Patients With Transthyretin (TTR)-Mediated Amyloidosis (ATTR Amyloidosis)


Sponsor

Alnylam Pharmaceuticals

Enrollment

1,500 participants

Start Date

Nov 23, 2020

Study Type

OBSERVATIONAL

Conditions

Summary

The purpose of this study is to: * Describe epidemiological and clinical characteristics, natural history and real-world clinical management of ATTR amyloidosis patients * Characterize the safety and effectiveness of patisiran and vutrisiran as part of routine clinical practice in the real-world clinical setting * Describe disease emergence/progression in pre-symptomatic carriers of a known disease-causing transthyretin (TTR) variant


Eligibility

Inclusion Criteria2

  • Diagnosis of ATTR amyloidosis or documented known disease-causing TTR variant for the cohort of pre-symptomatic carriers
  • Germany Only: Patients must be treated per the summary of product characteristics (SmPC) for any approved treatment for ATTR amyloidosis

Exclusion Criteria1

  • Current enrollment in a clinical trial for any investigational agent

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Locations(40)

Clinical Trial Site

La Jolla, California, United States

Clinical Trial Site

Los Angeles, California, United States

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Jacksonville, Florida, United States

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Iowa City, Iowa, United States

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Kansas City, Kansas, United States

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Baltimore, Maryland, United States

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Boston, Massachusetts, United States

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New York, New York, United States

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Durham, North Carolina, United States

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Columbus, Ohio, United States

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Philadelphia, Pennsylvania, United States

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Austin, Texas, United States

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Houston, Texas, United States

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Salvador, Brazil

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São Paulo, Brazil

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Sofia, Bulgaria

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Aarhus, Denmark

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Copenhagen, Denmark

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Bordeaux, France

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Bron, France

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Créteil, France

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Le Kremlin-Bicêtre, France

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Marseille, France

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Berlin, Germany

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Giessen, Germany

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Hanover, Germany

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Jerusalem, Israel

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Ramat Gan, Israel

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Milan, Italy

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Naples, Italy

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Palermo, Italy

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Roma, Italy

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Groningen, Netherlands

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Lisbon, Portugal

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Porto, Portugal

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Barcelona, Spain

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Madrid, Spain

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Palma, Spain

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New Taipei City, Taiwan

Clinical Trial Site

Taipei, Taiwan

View Full Details on ClinicalTrials.gov

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NCT04561518


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