RecruitingPhase 2NCT04793919

Treatment Study for Children and Adolescents With Acute Promyelocytic Leukemia


Sponsor

Associazione Italiana Ematologia Oncologia Pediatrica

Enrollment

89 participants

Start Date

Oct 9, 2019

Study Type

INTERVENTIONAL

Conditions

Summary

The trial is open to all patients with a diagnosis of acute promyelocytic leukemia (APL) who are PCR-positive for the PML-RARα transcript and less than 18 years of age.


Eligibility

Max Age: 18 Years

Inclusion Criteria3

  • Newly diagnosed APL confirmed by the presence of PML/RARα fusion gene
  • Age \<18 years
  • Written informed consent by parents or legal guardians

Exclusion Criteria9

  • Patients with a clinical diagnosis of APL but subsequently found to lack PML/RARα rearrangement should be withdrawn from the study and treated on an alternative protocol
  • Significant liver dysfunction (bilirubin serum levels \>3 mg/dL, ALT/AST serum levels greater than 5 times the normal values)
  • Creatinine serum levels \>2 times the normal value for age
  • Significant arrhythmias, EKG abnormalities (\*see below), other cardiac contraindications (L-FEV \<50% or LV-FS \<28%)
  • Neuropathy
  • Concurrent active malignancy
  • Uncontrolled life-threatening infections
  • Pregnant or lactating female
  • Patients who had received alternative therapy (APL not initially suspected; ATRA and/or ATO not available

Interventions

DRUGMylotarg

See the protocol

DRUGArsenic Trioxide

See the protocol

DRUGAll-trans retinoic acid

See the protocol


Locations(31)

Hôpital Universitaire des Enfants Reine Fabiola (Huderf)

Brussels, Belgium

University Hospital Motol

Prague, Czechia

Pediatrics and Adolescent Medicine Aarhus University Hospital

Aarhus N, Denmark

CHU de Bordeaux - Hôpital des Enfants

Bordeaux, France

Universitätsklinikum Essen (AöR) Zentrum für Kinder-und Jugendmedizin Klinik für Kinderheilkunde III

Essen, Germany

Our Lady's Children's Hospital Crumlin

Dublin, Ireland

Rappaport Children'S Hospital, Rambam Health Care Campus

Haifa, Israel

Ospedale "Casa Sollievo della Sofferenza" - UO Oncoematologia Pediatrica

San Giovanni Rotondo, Foggia, Italy

AOU Policlinico Dipartimento di Pediatria

Bari, Italy

Ospedale Papa Giovanni XXIII - USS Oncoematologia Pediatrica

Bergamo, Italy

AOU Policlinico Sant'Orsola-Malpighi - Oncologia ed Ematologia Pediatrica

Bologna, Italy

Ospedale Pediatrico Microcitemico "A.Cau", Az.Ospedaliera Brotzu - SC Oncoematologia Ped. e Patologia della coagulazione

Cagliari, Italy

AOU Policlinico Vittorio Emanuele - UOC Ematologia ed Oncologia Pediatrica con TNO

Catania, Italy

A.O. Universitaria Meyer - DAI Oncoematologia Pediatrica

Florence, Italy

IRCCS Istituto Gannina Gaslini - Dipartimento di Oncoematologia

Genova, Italy

Fondazione Monza e Brianza per il Bambino e la sua Mamma (MBBM) - Ospedale San Gerardo

Monza, Italy

AORN Santobono-Pausilipon

Napoli, Italy

Univerità degli Studi della Campania- Luigi Vanvitelli - Sevizio di Oncologia Pediatrica

Napoli, Italy

Azienda Ospedaliera di Padova - Oncoematologia Pediatrica

Padua, Italy

ARNAS Civico di Cristina e Benfratelli - UOC Oncoematologia Pediatrica

Palermo, Italy

Fondazione IRCCS Policlinico San Matteo - Oncoematologia Pediatrica

Pavia, Italy

Ospedale santa Chiara - AOU Pisana, UO Oncoematologia Pediatrica

Pisa, Italy

Policlinico Umberto I Università "LA Sapienza" - Dip. Biotecnologie cellulari ed ematologia UOS Ematologia Pediatrica

Roma, Italy

Dipartimento di Onco-Ematologia e Terapia Cellulare e Genica - Ospedale Pediatrico "Bambino Gesù"

Roma, Italy

AOU Città della Salute e della Scienza di Torino - Presidio Infantile Regina Margherita

Torino, Italy

VU medisch centrum

Amsterdam, Netherlands

Centro Hospitalar Universitário de Coimbra - Hospital Pediátrico de Coimbra

Coimbra, Portugal

Instituto Português de Oncologia de Lisboa Francisco Gentil, EPE

Lisbon, Portugal

Instituto Português de Oncologia do Porto Francisco Gentil, E. P. E.

Porto, Portugal

Valencia University Medical School University Hospital La Fe

Valencia, Spain

Childrens hematology and oncology Uppsala University

Uppsala, Sweden

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NCT04793919


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