RecruitingPhase 3NCT05066217

An Efficacy and Safety Study of Clemizole HCl in Patients With Lennox-Gastaut Syndrome

Multicenter, Randomized, Double-blind, Placebo-controlled Trial of Clemizole HCl as Adjunctive Therapy in Patients With Lennox-Gastaut Syndrome


Sponsor

Epygenix

Enrollment

260 participants

Start Date

Apr 9, 2025

Study Type

INTERVENTIONAL

Conditions

Summary

This is a multicenter, Phase 3, randomized, double-blind, placebo-controlled study designed to evaluate the efficacy and safety of clemizole HCL (EPX-100) as adjunctive therapy in children and adult participants with Lennox-Gastaut syndrome (LGS).


Eligibility

Min Age: 2 YearsMax Age: 55 Years

Inclusion Criteria7

  • Males or females, ages ≥2 to ≤55 years, at the time of Screening.
  • Participant/parent/legal authorized representative (LAR) willing and able to give written informed consent/assent.
  • Diagnosis of LGS, including:
  • Evidence of at least one type of countable major motor seizure.
  • History of electroencephalogram (EEG) consistent with LGS (abnormal background activity, and one of the following: 1) slow spike-wave discharges \[<2.5 Hz\], or 2) paroxysmal fast activity during sleep).
  • Abnormal cognitive development.
  • Onset of seizures at 11 years of age or younger.

Exclusion Criteria7

  • Known sensitivity, allergy, or previous exposure to clemizole HCl.
  • Known history of long QT syndrome or any significant history of a serious abnormality of the electrocardiogram (ECG) (e.g., recent myocardial infarction, clinically significant arrhythmia).
  • Family history of sudden cardiac death, unexplained death, or death from a primary dysrhythmia potentially associated with QT prolongation in any family member.
  • Seizures secondary to illicit drug or alcohol use, infection, neoplasm, demyelinating disease, degenerative neurological disease, or progressive central nervous system disease, metabolic illness, recent anoxic episode within the last 6 months requiring resuscitation, or progressive degenerative disease or any other condition, which in the opinion of the investigator, could affect seizure control.
  • Epilepsy surgery planned during the study or epilepsy surgery within 6 months prior to Screening.
  • Concomitant use of fenfluramine.
  • Prior or concomitant use of lorcaserin.

Interested in this trial?

Get notified about updates and connect with the research team.

Interventions

DRUGClemizole HCl

Clemizole HCl will be administered as an oral solution.

DRUGPlacebo

Placebo will be administered as an oral solution.


Locations(20)

Arkansas Children's Hospital

Little Rock, Arkansas, United States

UC Irvine Medical Center

Orange, California, United States

UCI Center for Innovative Health Therapies

Orange, California, United States

Nemours Children's Health

Wilmington, Delaware, United States

Rare Disease Research

Kissimmee, Florida, United States

University of Miami Miller School of Medicine

Miami, Florida, United States

Pediatric Neurology and Epilepsy Specialists

Winter Park, Florida, United States

Re:Cognition Health

Chicago, Illinois, United States

Norton Children's Medical Center

Louisville, Kentucky, United States

Henry Ford Hospital

Detroit, Michigan, United States

Minnesota Epilepsy Group, P.A.

Roseville, Minnesota, United States

Children's Nebraska

Omaha, Nebraska, United States

Neurology Center for Epilepsy and Seizures

Marlboro, New Jersey, United States

Tekton Research

Marlboro, New Jersey, United States

Weill Cornell Medicine/New York Presbyterian Hospital

New York, New York, United States

Atrium Health STRIVE Research

Charlotte, North Carolina, United States

On-Site Clinical Solution

Charlotte, North Carolina, United States

Duke University Medical Center

Durham, North Carolina, United States

PPD Virtual-Science 37, Inc.

Morrisville, North Carolina, United States

UTHealth Houston

Houston, Texas, United States

View Full Details on ClinicalTrials.gov

For the most up-to-date information, visit the official listing.

Visit

NCT05066217


Related Trials