RecruitingPhase 1Phase 2NCT05768139

First-in-Human Study of Tersolisib (STX-478) as Monotherapy and in Combination With Other Antineoplastic Agents in Participants With Advanced Solid Tumors

First-in-Human Study of STX-478, a Mutant-Selective PI3Kα Inhibitor as Monotherapy and in Combination With Other Antineoplastic Agents in Participants With Advanced Solid Tumors


Sponsor

Eli Lilly and Company

Enrollment

880 participants

Start Date

Apr 17, 2023

Study Type

INTERVENTIONAL

Conditions

Summary

Study STX-478-101 (LY4064809) is a multipart, open-label, phase 1/2 study evaluating the safety, tolerability, pharmacokinetics (PK), and preliminary antitumor activity of STX-478 (LY4064809) in participants with advanced solid tumors with P13Ka mutations. Part 1 will evaluate STX-478 as monotherapy in participants with advanced solid tumors. Part 2 will evaluate STX-478 therapy as combination therapy with fulvestrant in participants with hormone receptor positive (HR+) breast cancer. Part 3 will evaluate STX-478 as combination therapy with endocrine therapy (aromatase inhibitors, fulvestrant, tamoxifen, or imlunestrant) and a CDK4/6 Inhibitor (either Ribociclib, Palbociclib or Abemaciclib) in participants with HR+ breast cancer. Each study part will include a 28-day screening period, followed by treatment with STX-478 monotherapy or combination therapy.


Eligibility

Min Age: 18 Years

Plain Language Summary

Simplified for easier understanding

This study is testing STX-478, an investigational drug that targets a specific mutation in a gene called PI3K-alpha, in patients with advanced or spreading solid tumor cancers that no longer respond to standard treatments. **You may be eligible if...** - You are 18 or older - You have an advanced, metastatic, or locally advanced solid tumor cancer that has stopped responding to available treatments - Your tumor has a documented PI3K-alpha (PIK3CA) mutation - You are in good overall health (ECOG 0–1) - You have adequate organ function **You may NOT be eligible if...** - Your tumor does not have a PI3K-alpha mutation - You have had certain prior treatments that would interfere with this study - You have poor organ function or health status Talk to your doctor to see if this trial is right for you.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

DRUGSTX-478

STX-478 is a mutant-selective PI3Kα inhibitor

DRUGFulvestrant

Fulvestrant

DRUGRibociclib

Ribociclib

DRUGPalbociclib

Palbociclib

DRUGLetrozole

Letrozole

DRUGAnastrozole

Anastrozole

DRUGExemestane

Exemestane

DRUGTamoxifen

Tamoxifen

DRUGAbemaciclib

Abemaciclib

DRUGImlunestrant

Imlunestrant

DRUGMetformin

Metformin


Locations(66)

Ellison Clinic at Saint John's

Los Angeles, California, United States

UCSF Medical Center at Mission Bay

San Francisco, California, United States

University of Colorado Cancer Center

Aurora, Colorado, United States

Yale-New Haven Hospital

New Haven, Connecticut, United States

Florida Cancer Specialists ORLANDO/DDU

Lake Mary, Florida, United States

Moffitt Cancer Center

Tampa, Florida, United States

Winship Cancer Institute, Emory University

Atlanta, Georgia, United States

University of Iowa

Iowa City, Iowa, United States

Louisiana State University Health Sciences Center

New Orleans, Louisiana, United States

Massachusetts General Hospital

Boston, Massachusetts, United States

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Barbara Ann Karmanos Cancer Institute

Detroit, Michigan, United States

START Midwest

Grand Rapids, Michigan, United States

Saint Luke's Cancer Institute

Kansas City, Missouri, United States

Washington University

St Louis, Missouri, United States

Memorial Sloan Kettering Cancer Center

New York, New York, United States

UH Cleveland Medical Center

Cleveland, Ohio, United States

Stefanie Spielman Comprehensive Breast Center

Columbus, Ohio, United States

Providence Cancer Institute Franz Clinic

Portland, Oregon, United States

The West Clinic, PLLC dba West Cancer Center

Germantown, Tennessee, United States

Sarah Cannon Research Institute

Nashville, Tennessee, United States

Mary Crowley Cancer Research Center

Dallas, Texas, United States

Texas Oncology-Baylor Charles A. Sammons Cancer Center

Dallas, Texas, United States

University of Texas Southwestern

Dallas, Texas, United States

University of Texas MD Anderson Cancer Center

Houston, Texas, United States

START San Antonio

San Antonio, Texas, United States

START Mountain Region

West Valley City, Utah, United States

USO-Virginia Cancer Specialists, PC

Fairfax, Virginia, United States

Institut Jules Bordet

Anderlecht, Belgium

UZ Leuven

Leuven, Belgium

Institut Bergonié - Centre Régional de Lutte Contre Le Cancer de Bordeaux et Sud Ouest

Bordeaux, France

Centre Leon Berard

Lyon, France

Institut Paoli-Calmettes

Marseille, France

Centre Antoine-Lacassagne

Nice, France

Institut Claudius Regaud

Toulouse, France

Gustave Roussy

Villejuif, France

Universitätsklinikum Erlangen

Erlangen, Germany

Universitätsmedizin Mannheim

Mannheim, Germany

Mater Misericordiae Hospital

Dublin, Ireland

Azienda Ospedaliera Nazionale Santi Antonio e Biagio e Cesare Arrigo

Alessandria, Italy

Spedali Civili di Brescia

Brescia, Italy

Istituto Nazionale per lo Studio e la Cura dei Tumori

Milan, Italy

Istituto Europeo di Oncologia

Milan, Italy

Fondazione IRCCS San Gerardo dei Tintori

Monza, Italy

Azienda Ospedaliero Universitaria Pisana - Stabilimento Santa Chiara

Pisa, Italy

Ospedale Santa Maria delle Croci

Ravenna, Italy

Fondazione Policlinico Universitario Agostino Gemelli

Roma, Italy

Centro Ricerche Cliniche di Verona s.r.l.

Verona, Italy

National Hospital Organization Kyushu Cancer Center

Fukuoka, Japan

Kansai Medical University Hospital

Hirakata, Japan

The Cancer Institute Hospital of JFCR

Kōtō City, Japan

Kyoto University Hospital

Kyoto, Japan

Netherlands Cancer Institute

Amsterdam, Netherlands

Erasmus MC

Rotterdam, Netherlands

Hospital Quiron Barcelona

Barcelona, Spain

South Texas Accelerated Research Therapeutics (START) Barcelona- HM Nou Delfos

Barcelona, Spain

Instituto Oncologico Dr Rosell (IOR)

Barcelona, Spain

Hospital Universitari Vall d'Hebron

Barcelona, Spain

Hospital San Pedro

Logroño, Spain

MD Anderson Cancer Center

Madrid, Spain

Hospital Clinico San Carlos

Madrid, Spain

Hospital Universitario Fundación Jiménez Díaz

Madrid, Spain

Hospital Universitario HM Sanchinarro

Madrid, Spain

Hospital Universitario Quironsalud Madrid

Pozuelo de Alarcón, Spain

Hospital Universitari Sant Joan de Reus

Reus, Spain

Hospital Universitario Virgen Macarena

Seville, Spain

View Full Details on ClinicalTrials.gov

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NCT05768139


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