RecruitingNCT05769621

A Retrospective Study to Characterize Participants With Propionic Acidemia

A Retrospective Cohort Study to Characterize Propionic Acidemia Patients


Sponsor

ModernaTX, Inc.

Enrollment

60 participants

Start Date

Jun 16, 2023

Study Type

OBSERVATIONAL

Conditions

Summary

This is a non-interventional, observational, global, multicenter, study describing participant characteristics, clinical outcomes, and event rates in participants with propionic acidemia (PA).


Eligibility

Min Age: 2 Years

Plain Language Summary

Simplified for easier understanding

This clinical trial is studying a new treatment for people with propionic acidemia. The study is currently recruiting participants at 29 locations. People eligible for this study include aged 2 Years and older.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Locations(29)

University of Stanford Medical Center

Stanford, California, United States

Johns Hopkins University

Baltimore, Maryland, United States

University of Michigan Hospital

Ann Arbor, Michigan, United States

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Texas Children's Hospital

Houston, Texas, United States

Seattle Children's Hospital

Seattle, Washington, United States

Royal Children's Hospital Melbourne

Parkville, Victoria, Australia

Stollery Children's Hospital University of Alberta

Edmonton, Alberta, Canada

CHU Toulouse

Toulouse, Haute-Garonne, France

CHRU Nancy Hôpital des Enfants

Vandœuvre-lès-Nancy, Meurthe-et-Moselle, France

Hôpital Necker - Enfants Malades

Paris, Paris, France

CHU de Marseille - Hôpital de la Timone

Marseille, France

Azienda Ospedaliera Universitaria Federico II

Naples, Campania, Italy

ASST di Monza - Azienda Ospedaliera San Gerardo

Monza, Monza A Brianza, Italy

Azienda Ospedaliero Universitaria A Meyer - INCIPIT - PIN

Florence, Tuscany, Italy

Fujita Health University Hospital

Toyoake, Aichi-ken, Japan

The Jikei University School of Medicine

Minato, Tokyo, Japan

Erasmus MC

Rotterdam, South Holland, Netherlands

Hospital Sant Joan de Deu

Esplugues de Llobregat, Barcelona, Spain

Hospital Universitario Marques de Valdecilla

Santander, Cantabria, Spain

Hospital Universitario Cruces

Barakaldo, Spain

Hospital Universitario Raymon y Cajal

Madrid, Spain

Hospital Universitario 12 de Octubre

Madrid, Spain

Hospital Universitario Virgen del Rocio - PPDS

Seville, Spain

Hospital Universitari I Politecnic La Fe de Valencia

Valencia, Spain

Victoria Hospital

Kirkcaldy, Fife, United Kingdom

St Mary's Hospital - PPDS

Manchester, Lancashire, United Kingdom

Great Ormond Street Hospital

City of London, London, United Kingdom

University Hospital Birmingham

Birmingham, United Kingdom

View Full Details on ClinicalTrials.gov

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NCT05769621


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