RecruitingNCT05966467

Registry of Patients With AQP4+ NMOSD Treated With Alexion C5 Inhibitor Therapies

A Long-Term, Prospective, Observational, Registry of Patients With Anti-Aquaporin 4 Antibody-Positive (AQP4+) Neuromyelitis Optica Spectrum Disorder (NMOSD) Treated With Alexion Complement Component 5 (C5) Inhibitor Therapies (ALXN-C5IT)


Sponsor

Alexion Pharmaceuticals, Inc.

Enrollment

122 participants

Start Date

Feb 1, 2024

Study Type

OBSERVATIONAL

Conditions

Summary

Long-term, multicenter, multinational, observational, registry of patients with AQP4+ NMOSD that is designed to collect data on clinical outcomes and safety in patients prescribed Alexion C5 inhibitor therapies (C5IT). The registry will also collect data on patient reported outcomes (PROs), quality of life (QoL), and targeted AQP4+ NMOSD therapies used to provide evidence on the real-world impact of ALXN-C5IT on patients with AQP4+ NMOSD.


Eligibility

Min Age: 18 Years

Inclusion Criteria4

  • Participant is ≥ 18 years of age at the time of enrollment in the Registry.
  • Participant must have a confirmed diagnosis of AQP4+ NMOSD.
  • At the time of enrollment in the Registry, participants must be receiving treatment with ALXN-C5IT for the purpose of chronic relapse prevention in a manner consistent with the local label. Specifically, they should have received at least 1 dose of eculizumab within 4 weeks prior to enrollment or at least 1 dose of ravulizumab within 12 weeks prior to enrollment.
  • Participants must have both the following historical data available to be enrolled in the Registry: ALXN-C5IT dosing information since initiation and number and types of relapses from 1 year prior to ALXN-C5IT initiation through Registry enrollment.

Exclusion Criteria1

  • Participants currently enrolled in an interventional clinical study for the treatment of AQP4+ NMOSD in which the intervention is a drug.

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Locations(33)

Clinical Trial Site

Washington D.C., District of Columbia, United States

Research Site

Boston, Massachusetts, United States

Clinical Trial Site

Chapel Hill, North Carolina, United States

Clinical Trial Site

Columbus, Ohio, United States

Clinical Trial Site

Plano, Texas, United States

Clinical Trial Site

Milwaukee, Wisconsin, United States

Clinical Trial Site

Buenos Aires, Argentina

Clinical Trial Site

Buenos Aires, Argentina

Clinical Trial Site

Buenos Aires, Argentina

Clinical Trial Site

Buenos Aires, Argentina

Clinical Trial Site

Burnaby, British Columbia, Canada

Clinical Trial Site

Beijing, China

Clinical Trial Site

Guangzhou, China

Clinical Trial Site

Henan, China

Clinical Trial Site

Shanghai, China

Clinical Trial Site

Sichuan, China

Clinical Trial Site

Wuhan, China

Clinical Trial Site

Dresden, Germany

Clinical Trial Site

Essen, Germany

Clinical Trial Site

München, Germany

Clinical Trial Site

Naples, Italy

Clinical Trial Site

Fukuoka, Japan

Clinical Trial Site

Kawasaki, Japan

Clinical Trial Site

Miyagi, Japan

Clinical Trial Site

Tokyo, Japan

Clinical Trial Site

Daejeon, South Korea

Clinical Trial Site

Gyeonggi-do, South Korea

Clinical Trial Site

Seoul, South Korea

Clinical Trial Site

Seoul, South Korea

Clinical Trial Site

Seoul, South Korea

Clinical Trial Site

Seoul, South Korea

Clinical Trial Site

Seoul, South Korea

Clinical Trial Site

Seoul, South Korea

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NCT05966467


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