RecruitingPhase 3NCT06229210

Safety and Tolerability Trial of Lumateperone in Pediatric Patients With Schizophrenia, Bipolar Disorder or Autism Spectrum Disorder

An Open-label, Multicenter Trial to Assess the Safety and Tolerability of Lumateperone in the Treatment of Pediatric Patients With Schizophrenia, Bipolar Disorder or Autism Spectrum Disorder


Sponsor

Intra-Cellular Therapies, Inc.

Enrollment

500 participants

Start Date

Jan 25, 2024

Study Type

INTERVENTIONAL

Conditions

Summary

This is a multicenter, global, 26-week, open-label study to assess the safety and tolerability of lumateperone in pediatric patients with schizophrenia, bipolar disorder or autism spectrum disorder.


Eligibility

Min Age: 5 YearsMax Age: 17 Years

Inclusion Criteria7

  • Able to provide consent as follows:
  • The patient's legally authorized representative (LAR) (eg, parent or guardian) must provide written, informed consent;
  • The patient must provide written assent to study enrollment;
  • Male or female patients aged 13 to 17 years (inclusive) with schizophrenia; male or female patients aged 10 to 17 years (inclusive) with bipolar I or II disorder; or male or female patients aged 5 to 17 years (inclusive) with autism spectrum disorder;
  • Meet Diagnostic and Statistical Manual of Mental Disorders, Fifth Edition Text Revision (DSM-5-TR) primary diagnosis of schizophrenia, bipolar I or II disorder, or autism spectrum disorder as confirmed by Kiddie Schedule for Affective Disorders and Schizophrenia for School-Age Children-Present and Lifetime Version (K-SADS-PL).
  • Is currently an outpatient and is anticipated to maintain outpatient status for the duration of the study.
  • Rollover Patients entering from the lead-in study must have safely completed the lead-in study, in the opinion of the Investigator.

Exclusion Criteria8

  • Has a primary psychiatric diagnosis other than schizophrenia, bipolar I or bipolar II disorder or autism spectrum disorder. Schizophrenia with catatonia, or bipolar disorder with psychotic features are not allowed. Exceptions include:
  • ADHD: If a subject is taking psychostimulant(s) for ADHD, they must have been on a stable treatment regimen of these medication(s) for 30 days prior to Screening. The treatment regimen should remain stable throughout the study. This must be confirmed by the Investigator and noted in the source records.
  • For ASD patients only, based on Investigator opinion and DSM-5 criteria, mild or moderate intellectual disability is allowed. Severe or profound intellectual disability is exclusionary.
  • In the opinion of the Investigator, the patient has a significant risk for suicidal behavior during their participation in the study or
  • At Screening, the patient scores "yes" on Suicidal Ideation Items 3, 4, or 5 of the Columbia-Suicide Severity Rating Scale (C SSRS) within 6 months prior to Screening or, at Baseline, the patient scores "yes" on Suicidal Ideation Items 3, 4, or 5 since the Screening Visit;
  • At Screening, the patient has had 1 or more suicidal attempts within the 2 years prior to Screening; or
  • At Screening or Baseline, scores \> 3 on Item 13 (suicidal ideation) of the CDRS-R (for bipolar disorder patients only); or
  • The patient is considered to be an imminent danger to him/herself or others.

Interventions

DRUGLumateperone

Lumateperone 5 mg - 42 mg capsules or orally disintegrating tablets administered orally, once daily based on age and indication


Locations(50)

Clinical Site

Phoenix, Arizona, United States

Clinical Site

Little Rock, Arkansas, United States

Clinical Site

Anaheim, California, United States

Clinical Site

Colton, California, United States

Clinical Site

Garden Grove, California, United States

Clinical Site

Long Beach, California, United States

Clinical Site

Redlands, California, United States

Clinical Site

San Diego, California, United States

Clinical Site

West Covina, California, United States

Clinical Site

Colorado Springs, Colorado, United States

Clinical Site

Gainesville, Florida, United States

Clinical Site

Hialeah, Florida, United States

Clinical Site

Miami, Florida, United States

Clinical Site

Miami, Florida, United States

Clinical Site

Miami, Florida, United States

Clinical Site

Miami, Florida, United States

Clinical Site

Miami, Florida, United States

Clinical Site

Miami, Florida, United States

Clinical Site

Miami, Florida, United States

Clinical Site

Miami Gardens, Florida, United States

Clinical Site

Miami Lakes, Florida, United States

Clinical Site

Miami Lakes, Florida, United States

Clinical Site

Miami Springs, Florida, United States

Clinical Site

Orlando, Florida, United States

Clinical Site

Pompano Beach, Florida, United States

Clinical Site

West Palm Beach, Florida, United States

Clinical Site

Atlanta, Georgia, United States

Clinical Site

Decatur, Georgia, United States

Clinical Site

Lawrenceville, Georgia, United States

Clinical Site

Savannah, Georgia, United States

Clinical Site

Naperville, Illinois, United States

Clinical Site

Indianapolis, Indiana, United States

Clinical Site

Bloomfield Hills, Michigan, United States

Clinical Site

Saint Charles, Missouri, United States

Clinical Site

Lincoln, Nebraska, United States

Clinical Site

Las Vegas, Nevada, United States

Clinical Site

Avon Lake, Ohio, United States

Clinical Site

Cincinnati, Ohio, United States

Clinical Site

Garfield, Ohio, United States

Clinical Site

Oklahoma City, Oklahoma, United States

Clinical Site

Fort Worth, Texas, United States

Clinical Site

Houston, Texas, United States

Clinical Site

Plano, Texas, United States

Clinical Site

Richmond, Texas, United States

Clinical Site

Richmond, Virginia, United States

Clinical Site

Bellevue, Washington, United States

Clinical Site

Everett, Washington, United States

Clinical Site

Belgrade, Serbia

Clinical Site

Niš, Serbia

Clinical Site

Novi Sad, Serbia

View Full Details on ClinicalTrials.gov

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NCT06229210


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