RecruitingPhase 2NCT06237335

A Phase 2 Study Evaluating Safety and Tolerability of RCT2100 (CFTR mRNA) in Healthy Participants and in Participants With CF

A Phase 1/2, Multicenter Study Evaluating the Safety, Tolerability, and Biodistribution of RCT2100 With Single-Ascending Doses in Healthy Participants and Multiple-Ascending Doses and Proof-of-Concept in Participants With Cystic Fibrosis


Sponsor

ReCode Therapeutics

Enrollment

192 participants

Start Date

Feb 1, 2024

Study Type

INTERVENTIONAL

Conditions

Summary

This is the first-in-human study with RCT2100 and is designed to provide safety and tolerability data for future clinical studies.


Eligibility

Min Age: 18 YearsMax Age: 60 Years

Plain Language Summary

Simplified for easier understanding

This clinical trial is studying a drug called Ivacaftor, Placebo, and others for people with cystic fibrosis. The study is currently recruiting participants at 23 locations. People eligible for this study include aged 18 Years to 60 Years.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

DRUGRCT2100

RCT2100 supplied as varying dose strengths administered via oral inhalation using nebulizer

OTHERPlacebo

Placebo of similar volumes to experimental dose strengths administered via oral inhalation using nebulizer

DRUGRCT2100

RCT2100 supplied as varying dose strengths administered via oral inhalation using nebulizer for 4 weeks

DRUGRCT2100

RCT2100 supplied at a single dose strength administered via oral inhalation using nebulizer for 12 weeks

DRUGIvacaftor

ivacaftor administered orally for 6 weeks

DRUGRCT2100

RCT2100 supplied at varying dose strengths. Co- administered via oral inhalation using nebulizer for 4 weeks with ivacaftor after initial 2 weeks of ivacaftor dosing run in period


Locations(23)

The University of Alabama at Birmingham

Birmingham, Alabama, United States

University of Arizona

Tucson, Arizona, United States

Stanford University

Palo Alto, California, United States

UCSD

San Diego, California, United States

National Jewish Health

Denver, Colorado, United States

Emory University

Atlanta, Georgia, United States

Boston Children's Hospital

Boston, Massachusetts, United States

New York Medical College

Valhalla, New York, United States

The University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

Oregon Health & Science University

Portland, Oregon, United States

University of Pittsburgh

Pittsburgh, Pennsylvania, United States

UT Southwestern Medical Center

Dallas, Texas, United States

University of Washington

Seattle, Washington, United States

Centre Hospitalier Régional Universitaire de Montpellier - Hôpital Arnaud de Villeneuve

Montpellier, France

Hôpital Necker Enfants Malades

Paris, France

UMC Utrecht

Utrecht, Netherlands

New Zealand Clinical Research (Part 1 Only)

Auckland, New Zealand

University Hospitals Birmingham

Birmingham, United Kingdom

Royal Papworth Hospital

Cambridge, United Kingdom

Leeds Teaching Hospitals

Leeds, United Kingdom

King's College Hospital

London, United Kingdom

Nottingham University Hospitals

Nottingham, United Kingdom

University Hospital Southampton

Southampton, United Kingdom

View Full Details on ClinicalTrials.gov

For the most up-to-date information, visit the official listing.

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NCT06237335


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