RecruitingPhase 2NCT06369285

A Study of Alisertib in Combination With Endocrine Therapy in Patients With HR-positive, HER2-negative Recurrent or Metastatic Breast Cancer

A Phase 2 Study of Alisertib in Combination With Endocrine Therapy in Patients With HR+, HER2-negative Recurrent or Metastatic Breast Cancer


Sponsor

Puma Biotechnology, Inc.

Enrollment

150 participants

Start Date

Nov 19, 2024

Study Type

INTERVENTIONAL

Conditions

Summary

PUMA-ALI-1201 is a randomized, dose optimization, multicenter, Phase 2 study of alisertib administered in combination with endocrine therapy in participants with pathology-confirmed HR-positive/HER2-negative metastatic breast cancer (MBC) following progression on or after at least two prior lines of endocrine therapy in the recurrent or metastatic setting. This study is intended to evaluate the optimal alisertib dose administered in combination with the selected endocrine therapy. The study is also planned to evaluate the efficacy, safety, and pharmacokinetics of alisertib in combination with endocrine and to identify the biomarker-defined subgroup(s) that may benefit most from combined alisertib and endocrine therapy.


Eligibility

Min Age: 18 Years

Inclusion Criteria5

  • Aged ≥18 years at signing of informed consent.
  • Pathology-confirmed diagnosis of adenocarcinoma of the breast with evidence of recurrent or metastatic disease not amenable to curative therapy.
  • Progression on or after treatment with at least two prior lines of endocrine therapy in the recurrent or metastatic setting. a. If metastatic disease recurrence occurs during or within six months of discontinuing adjuvant endocrine therapy, then that endocrine therapy will count as one line of prior therapy.
  • Participants must have received a CDK4/6i in combination with endocrine therapy in the recurrent or metastatic setting.
  • HR-positive and HER2-negative tumor status reported per local laboratory testing. HR and HER2 testing must be performed consistent with current American Society of Clinical Oncology/College of American Pathologists (ASCO/CAP) or European Society of Medical Oncology (ESMO) guidelines:

Exclusion Criteria2

  • Treatment with chemotherapy in the recurrent or metastatic setting.
  • Prior treatment with an Aurora Kinase A (AURKA) specific-targeted or pan-Aurora-targeted agent, including alisertib, in any setting.

Interventions

DRUGAlisertib

Alisertib enteric-coated tablets will be taken by mouth twice daily on days 1-3, 8-10, and 15-17 of each 28-day cycle.

DRUGEndocrine therapy

Investigator selected endocrine therapy will be taken in 28-day dosing cycles according to the approved prescribing information. 1 mg of anastrozole tablet by mouth once daily or 2.5 mg of letrozole tablet by mouth once daily or 25 mg of exemestane tablet by mouth once daily or 20 mg of tamoxifen tablet by mouth once daily or 500 mg of fulvestrant intramuscular injection on Study Day 1, 15, 29, and once every 28 days thereafter


Locations(53)

Alabama Oncology

Birmingham, Alabama, United States

Mayo Clinic Hospital

Phoenix, Arizona, United States

Beverly Hills Cancer Center

Beverly Hills, California, United States

MemorialCare Orange Coast Medical Center

Fountain Valley, California, United States

City of Hope at Orange County Lennar Foundation Cancer Center

Irvine, California, United States

LA Cancer Network

Los Angeles, California, United States

UCLA Department of Medicine - Hematology/Oncology

Los Angeles, California, United States

University of California San Francisco (UCSF) Helen Diller Family Comprehensive Cancer Center

San Francisco, California, United States

University of Colorado School of Medicine

Aurora, Colorado, United States

Yale University, Yale Cancer Center

New Haven, Connecticut, United States

Mayo Clinic Florida

Jacksonville, Florida, United States

Cancer Specialists of North Florida

Jacksonville, Florida, United States

Moffitt Cancer Center

Tampa, Florida, United States

Winship Cancer Institute, Emory University

Atlanta, Georgia, United States

University of Illinois Cancer Center

Chicago, Illinois, United States

The University of Chicago

Chicago, Illinois, United States

Massachusetts General Hospital

Boston, Massachusetts, United States

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

University of Minnesota, Masonic Cancer Center

Minneapolis, Minnesota, United States

Mayo Clinic

Rochester, Minnesota, United States

Missouri Cancer Associates

Columbia, Missouri, United States

Saint Luke's Cancer Institute

Kansas City, Missouri, United States

Oncology Hematology Associates

Springfield, Missouri, United States

Washington University School of Medicine

St Louis, Missouri, United States

Cancer Care Specialists

Reno, Nevada, United States

University of Rochester Medical Center

Rochester, New York, United States

UNC Hospitals, University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

The Ohio State University, Stefanie Spielman Comprehensive Breast Center

Columbus, Ohio, United States

Taylor Cancer Research Center

Maumee, Ohio, United States

Alliance Cancer Specialists

Horsham, Pennsylvania, United States

University of Pennsylvania, Abramson Cancer Center, Perelman Center for Advanced Medicine

Philadelphia, Pennsylvania, United States

University of Pittsburgh (UPMC)

Pittsburgh, Pennsylvania, United States

Tennessee Oncology, Greco-Hainsworth Center for Research

Nashville, Tennessee, United States

Texas Oncology

Dallas, Texas, United States

Virginia Cancer Institute

Richmond, Virginia, United States

Instituto Português de Oncologia de Lisboa Francisco Gentil (IPO Lisboa)

Lisbon, Portugal

Fundação Champalimaud

Lisbon, Portugal

Hospital CUF Descobertas

Lisbon, Portugal

Instituto Português Oncologia Do Porto

Porto, Portugal

Hospital General Universitario Dr. Balmis

Alicante, Spain

Hospital Universitario de Cruces

Barakaldo, Spain

Hospital Universitario Vall d'Hebron

Barcelona, Spain

Hospital Clínico de Barcelona

Barcelona, Spain

Hospital Universitario de Basurto

Bilbao, Spain

Hospital San Pedro de Alcántara

Cáceres, Spain

Hospital San Cecilio

Granada, Spain

Hospital Universitario Juan Ramon Jimenez

Huelva, Spain

Hospital Universitario de Jaén

Jaén, Spain

Hospital Universitario Arnau de Vilanova

Lleida, Spain

Hospital Universitario Fundación Jiménez Díaz

Madrid, Spain

Hospital Universitario Virgen del Rocío

Seville, Spain

Fundación Instituto Valenciano de Oncología (IVO)

Valencia, Spain

Hospital Clínico Universitario de Valencia

Valencia, Spain

View Full Details on ClinicalTrials.gov

For the most up-to-date information, visit the official listing.

Visit

NCT06369285


Related Trials