RecruitingPhase 2Phase 3NCT06392386

A Study of Efgartigimod PH20 SC in Children Between 2 and Less Than 18 Years of Age With Generalized Myasthenia Gravis

An Open-label, Uncontrolled Study to Evaluate the Pharmacokinetics, Pharmacodynamics, Safety, and Activity of Efgartigimod PH20 SC in Participants From 2 to Less Than 18 Years of Age With Generalized Myasthenia Gravis


Sponsor

argenx

Enrollment

12 participants

Start Date

Jun 28, 2024

Study Type

INTERVENTIONAL

Conditions

Summary

The purpose of this study is to measure the pharmacokinetics (PK), pharmacodynamics (PD), safety, tolerability, and immunogenicity of efgartigimod PH20 SC in pediatric participants with gMG aged 2 to \<18 years. The primary goal is to confirm an appropriate dose of efgartigimod PH20 SC for pediatric patients using PK and PD results from this study. Participants will receive injections of efgartigimod PH20 SC and will be monitored for safety until the end of the study. At the end of the follow-up period, eligible participants may roll over to an open-label extension (OLE) study. The participants will be in the study for up to 14 weeks.


Eligibility

Min Age: 2 YearsMax Age: 17 Years

Plain Language Summary

Simplified for easier understanding

This clinical trial is studying a biological treatment called Efgartigimod PH20 SC for people with generalized myasthenia gravis. The study is currently recruiting participants at 20 locations.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

BIOLOGICALEfgartigimod PH20 SC

Subcutaneous injections


Locations(20)

Carolinas HealthCare System Neurosciences Institute - Neurology

Charlotte, North Carolina, United States

Neurology Rare Disease Center

Denton, Texas, United States

University of Virginia

Charlottesville, Virginia, United States

UZ Gent

Ghent, Belgium

Childrens Hospital of Eastern Ontario

Ottawa, Canada

Fakultni nemocnice Brno

Brno, Czechia

Fakultni nemocnice Ostrava

Ostrava, Czechia

AP-HM- Hôpital de La Timone

Marseille, France

Universitätsklinikum Essen

Essen, Germany

Hadassah Medical Center- Ein Kerem

Jerusalem, Israel

Schneider Children's Medical Center of Israel

Petah Tikvah, Israel

Tel Aviv Sourasky Medical Center Ichilov

Tel Aviv, Israel

Istituto G Gaslini Ospedale Pediatrico IRCCS

Genova, Italy

Leiden University Medical Center

Leiden, Netherlands

Uniwersyteckie Centrum Kliniczne w Gdansku

Gdansk, Poland

Neurologia Śląska Centrum Medyczne

Katowice, Poland

Centralny Szpital Kliniczny - Uniwersyteckie Centrum Kliniczne WUM

Warsaw, Poland

Hospital Universitari i Politecnic La Fe de Valencia

Valencia, Spain

Hôpital Nestlé

Lausanne, Switzerland

Oxford Children's Hospital

Oxford, United Kingdom

View Full Details on ClinicalTrials.gov

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NCT06392386


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