RecruitingPhase 3NCT06439082

A Study to Investigate the Efficacy and Safety of Crizanlizumab (5 mg/kg) Compared With Placebo in Adolescent and Adult Sickle Cell Disease Patients Who Experience Frequent Vaso-Occlusive Crises (SPARKLE)

A Phase III, Multicenter, Randomized, Placebo Controlled, Double-blind Study to Assess Efficacy and Safety of Crizanlizumab (5 mg/kg) Versus Placebo, With or Without Hydroxyurea/Hydroxycarbamide Therapy, in Adolescent and Adult Sickle Cell Disease Patients With Frequent Vaso-Occlusive Crises


Sponsor

Novartis Pharmaceuticals

Enrollment

354 participants

Start Date

Oct 24, 2024

Study Type

INTERVENTIONAL

Conditions

Summary

A phase III, multi-center, randomized, placebo-controlled, double-blind study to assess efficacy and safety of crizanlizumab (5 mg/kg) versus placebo, with or without hydroxyurea/hydroxycarbamide therapy, in adolescent and adult Sickle Cell Disease patients with frequent vaso-occlusive crises.


Eligibility

Min Age: 12 YearsMax Age: 100 Years

Plain Language Summary

Simplified for easier understanding

This clinical trial is studying a biological treatment called Crizanlizumab and a drug called Placebo for people with sickle cell disease. The study is currently recruiting participants at 32 locations. People eligible for this study include aged 12 Years to 100 Years.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

BIOLOGICALCrizanlizumab

Crizanlizumab is supplied in single use 10 mL glass vials at a concentration of 10 mg/mL. One vial contains 100 mg of crizanlizumab. This is a concentrate for solution for IV infusion.

DRUGPlacebo

Placebo is supplied in single use 10 mL glass vials at a concentration of 0 mg/mL. This is a concentrate for solution for IV infusion.


Locations(32)

University Of Alabama

Birmingham, Alabama, United States

Ctr for Inherited Blood Disorders

Orange, California, United States

Childrens National Hospital

Washington D.C., District of Columbia, United States

University of Florida

Jacksonville, Florida, United States

Augusta University Georgia

Augusta, Georgia, United States

WCG Sonar Clinical Research

Riverdale, Georgia, United States

Norton Children s Hospital

Louisville, Kentucky, United States

The Johns Hopkins University School of Medicine

Baltimore, Maryland, United States

Southern Specialty Research

Flowood, Mississippi, United States

Childrens Hospital at Montefiore

The Bronx, New York, United States

East Carolina University

Greenville, North Carolina, United States

Wake Forest University Baptist Medical Center

Winston-Salem, North Carolina, United States

Spoknwrdclinicaltrials

Easton, Pennsylvania, United States

U of TX Health Science Ct

Houston, Texas, United States

Novartis Investigative Site

Salvador, Estado de Bahia, Brazil

Novartis Investigative Site

São Luís, Maranhão, Brazil

Novartis Investigative Site

Campinas, São Paulo, Brazil

Novartis Investigative Site

Ribeirão Preto, São Paulo, Brazil

Novartis Investigative Site

Sao Jose Rio Preto, São Paulo, Brazil

Novartis Investigative Site

São Paulo, São Paulo, Brazil

Novartis Investigative Site

São Paulo, São Paulo, Brazil

Novartis Investigative Site

Medellín, Antioquia, Colombia

Novartis Investigative Site

Cali, Valle del Cauca Department, Colombia

Novartis Investigative Site

Cali, Valle del Cauca Department, Colombia

Novartis Investigative Site

Montería, Colombia

Novartis Investigative Site

Ahero, Kisumu County, Kenya

Novartis Investigative Site

Kisumu, Kenya

Novartis Investigative Site

Kisumu, Kenya

Novartis Investigative Site

Siaya, Kenya

Novartis Investigative Site

Kampala, Uganda

Novartis Investigative Site

Masaka, Uganda

Novartis Investigative Site

Tororo, Uganda

View Full Details on ClinicalTrials.gov

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NCT06439082


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