RecruitingPhase 1Phase 2NCT07599176

Partial Stem Cell Transplant for Sickle Cell Disease From Matched Donors

Matched Related Donor Non-myeloablative Hematopoietic Cell Transplantation With Alemtuzumab, 400 cGy TBI, and Abatacept for Sickle Cell Disease and Beta-Thalassemia


Sponsor

National Heart, Lung, and Blood Institute (NHLBI)

Enrollment

90 participants

Start Date

Jul 8, 2026

Study Type

INTERVENTIONAL

Conditions

Summary

This is a non-ablative (partial) stem cell transplant for patients with severe sickle cell disease or beta-thalassemia requiring red cell transfusions. The intensity of the transplant is slightly increased from our previous transplant regimens. The goal is to aim for higher percentage of donor cells to stably remain in the recipients long term.


Eligibility

Min Age: 4 YearsMax Age: 65 Years

Plain Language Summary

Simplified for easier understanding

This clinical trial is studying a drug called Abatacept, a drug called Alemtuzumab, and others for people with beta-thalassemia and sickle cell disease. The study is currently recruiting participants at 1 location. People eligible for this study include aged 4 Years to 65 Years.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

RADIATIONTotal Body Irradiation

Total Body Irradiation 400 cGy

DRUGAlemtuzumab

1 mg/kg

DRUGAbatacept

10 mg/kg x 6

OTHERResearch blood draw

About 5 tablespoons of blood will be collected from donors for research purposes.


Locations(1)

National Institutes of Health Clinical Center

Bethesda, Maryland, United States

View Full Details on ClinicalTrials.gov

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NCT07599176


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