RecruitingPhase 1NCT06600321

A Study to Evaluate ALN-BCAT in Patients With Hepatocellular Carcinoma

A Phase 1 Study of ALN-BCAT as Monotherapy and in Combination With Pembrolizumab in Patients With Advanced or Metastatic Hepatocellular Carcinoma


Sponsor

Alnylam Pharmaceuticals

Enrollment

158 participants

Start Date

Dec 30, 2024

Study Type

INTERVENTIONAL

Conditions

Summary

The purpose of the dose escalation part of the study is to characterize the safety and tolerability of ALN-BCAT as monotherapy and in combination with pembrolizumab; and to determine the recommended dose(s) for expansion (RDFE) of ALN-BCAT as monotherapy and in combination with pembrolizumab. The purpose of the dose expansion part of the of the study is to evaluate the antitumor activity of ALN-BCAT as monotherapy and in combination with pembrolizumab; to characterize the safety and tolerability of ALN-BCAT as monotherapy and in combination with pembrolizumab.


Eligibility

Min Age: 18 Years

Inclusion Criteria4

  • Has HCC confirmed histologically or cytologically, or, for patients with liver cirrhosis, clinically by the American Association for the Study of Liver Diseases (AASLD) criteria
  • Has had at least one line of systemic therapy for unresectable advanced or metastatic disease
  • Has at least one wingless-related integration site (WNT)-pathway activating mutation
  • Child-Pugh class A or B7

Exclusion Criteria3

  • Has fibrolamellar HCC, sarcomatoid HCC, or mixed cholangio-HCC tumors
  • Has symptomatic extrahepatic disease
  • Has received anti-cancer therapy or investigational drugs ≤3 weeks prior to the first dose of study drug

Interventions

DRUGALN-BCAT

Administered by intravenous (IV) infusion

DRUGPembrolizumab

Administered by intravenous (IV) infusion


Locations(23)

Clinical Trial Site

Phoenix, Arizona, United States

Clinical Trial Site

La Jolla, California, United States

Clinical Trial Site

Los Angeles, California, United States

Clinical Trial Site

Jacksonville, Florida, United States

Clinical Trial Site

Atlanta, Georgia, United States

Clinical Trial Site

Chicago, Illinois, United States

Clinical Trial Site

Ann Arbor, Michigan, United States

Clinical Trial Site

Rochester, Minnesota, United States

Clinical Trial Site

New York, New York, United States

Clinical Trial Site

New York, New York, United States

Clinical Trial Site

Cleveland, Ohio, United States

Clinical Trial Site

Pittsburgh, Pennsylvania, United States

Clinical Trial Site

Dallas, Texas, United States

Clinical Trial Site

Houston, Texas, United States

Clinical Trial Site

San Antonio, Texas, United States

Clinical Trial Site

Richmond, Virginia, United States

Clinical Trial Site

Milan, Italy

Clinical Trial Site

Rozzano, Italy

Clinical Trial Site

Verona, Italy

Clinical Trial Site

Busan, South Korea

Clinical Trial Site

Seongnam, South Korea

Clinical Trial Site

Seongnam, South Korea

Clinical Trial Site

Seoul, South Korea

View Full Details on ClinicalTrials.gov

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NCT06600321


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