RecruitingPhase 2NCT06747858

Safety, Tolerability and Efficacy Study of ARCT-032 in People With Cystic Fibrosis

A Phase 2, Open-label, Multiple Ascending-Dose Study to Evaluate the Safety, Tolerability and Efficacy of ARCT-032 in People With Cystic Fibrosis


Sponsor

Arcturus Therapeutics, Inc.

Enrollment

12 participants

Start Date

Dec 12, 2024

Study Type

INTERVENTIONAL

Conditions

Summary

ARCT-032-02 is a Phase 2, open-label, multicenter, multiple-ascending dose study of ARCT-032 in adults with CF who are not eligible for CFTR modulator therapy or are not taking CFTR modulators due to drug intolerance, poor response, or lack of access to modulators.


Eligibility

Min Age: 18 Years

Inclusion Criteria3

  • Confirmed diagnosis of Cystic Fibrosis
  • Not eligible for CFTR modulator therapy, or not taking CFTR modulators for at least 60 days prior to dosing (e.g. due to intolerance, poor response, or lack of access to modulators).
  • FEV1 between 40% and 100% of predicted value

Exclusion Criteria7

  • History of illness or medical condition that might pose an additional risk or may confound study results
  • Recent moderate or severe hemoptysis
  • Recent major surgery
  • Solid organ or hematologic transplant
  • Requirement of supplemental oxygen while awake or > 2L per minute while sleeping.
  • Chronic maintenance systemic corticosteroids exceeding equivalent of daily 15 mg oral prednisone or 30 mg every other day
  • Adequate liver and kidney function as determined by lab tests

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Interventions

BIOLOGICALARCT-032

CFTR mRNA formulated in lipid nanoparticles


Locations(11)

University of Arizona

Tucson, Arizona, United States

University of Arkansas for Medical Sciences

Little Rock, Arkansas, United States

Children's Hospital of Los Angeles

Los Angeles, California, United States

Joe DiMaggio Children's Hospital

Hollywood, Florida, United States

Central Florida Pulmonary Group

Orlando, Florida, United States

The Cystic Fibrosis Institute

Northfield, Illinois, United States

Boston Children's Hospital

Boston, Massachusetts, United States

Washington University

St Louis, Missouri, United States

Vanderbilt University

Nashville, Tennessee, United States

UT Health

San Antonio, Texas, United States

Seattle Children's Hospital

Seattle, Washington, United States

View Full Details on ClinicalTrials.gov

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NCT06747858


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