RecruitingPhase 3NCT06813911

Lp(a) Lowering Study of Pelacarsen (TQJ230) With Background Inclisiran in Participants With Elevated Lp(a) and Established ASCVD

A Randomized, Double-blind, Placebo-controlled, Multicenter Study to Evaluate the Efficacy, Safety, and Tolerability of Pelacarsen (TQJ230) With Background Inclisiran in Participants With Atherosclerotic Cardiovascular Disease (ASCVD), and Elevated LDL-C and Lp(a)


Sponsor

Novartis Pharmaceuticals

Enrollment

340 participants

Start Date

Apr 30, 2025

Study Type

INTERVENTIONAL

Conditions

Summary

The purpose of the study CTQJ230A12304, is to evaluate the efficacy, safety, and tolerability of pelacarsen (TQJ230) compared to placebo in participants with ASCVD who have elevated lipoprotein(a) (Lp(a)), and who are on background inclisiran treatment for elevated low-density lipoprotein cholesterol (LDL-C).


Eligibility

Min Age: 18 YearsMax Age: 80 Years

Inclusion Criteria7

  • Male and female participants 18 to ≤80 years of age at Screening visit
  • Established ASCVD, defined as documented coronary heart disease (CHD), cerebrovascular disease (CVD), or peripheral arterial disease (PAD) at Screening visit
  • On stable dose of local guideline recommended lipid lowering therapy for at least 30 days prior to Screening visit
  • Participants must successfully complete the run-in period of background inclisiran treatment in order to be randomized
  • On standard of care (SoC) treatment for other CVD risk factors including hypertension and diabetes for at least 30 days prior to Randomization/Baseline visit
  • Central laboratory reported Lp(a) ≥175 nmol/L at Screening visit
  • Central laboratory reported LDL-C \>70 mg/dL (or \>1.8 mmol/L) at Screening visit

Exclusion Criteria12

  • Prior treatment with inclisiran
  • Any other PCSK9 inhibitor (e.g., evolocumab, alirocumab) use within 4 months prior to Screening visit
  • Uncontrolled hypertension at Randomization/Baseline visit
  • Heart failure New York Heart Association (NYHA) class IV at Screening visit or at Randomization/Baseline visit (Day 1)
  • Triglycerides ≥400 mg/dL at Screening visit
  • History of malignancy of any organ system within the past 5 years
  • Myocardial infarction, stroke or other major bleeding, coronary or lower limb re vascularization, major cardiac or non-cardiac surgery between Screening visit and Randomization/Baseline visit (Day 1)
  • Central laboratory reported platelet count \<140,000 per mm3
  • Active liver disease or hepatic dysfunction at Screening visit
  • Significant kidney disease at Screening visit
  • Pregnant or nursing women at Screening visit
  • Any uncontrolled chronic or serious medical condition which may pose an immediate risk to clinical stability of the study participant at Screening visit

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Interventions

DRUGPelacarsen

Pelacarsen will be provided as solution for injection in prefilled syringe 80 mg for subcutaneous injection.

DRUGPlacebo

Placebo will be provided as solution for injection in prefilled syringe for subcutaneous injection.

DRUGInclisiran

All participants will be administered two loading doses of inclisiran as background treatment at Run-in 1 and Run-in 2, separated by 3 months, according to the approved label. After that inclisiran will be administered every 6 months, i.e., Month 5 and Month 11.


Locations(80)

Parkway Medical Center

Birmingham, Alabama, United States

Clinical Research Inst of Arizona

Sun City West, Arizona, United States

National Heart Institute

Beverly Hills, California, United States

Interv Cardiology Med Grp

West Hills, California, United States

Excel Medical Clinical Trials LLC

Boca Raton, Florida, United States

Jacksonville Center for Clinical

Jacksonville, Florida, United States

K2 Medical Research LLC

Maitland, Florida, United States

University of Miami Hospital

Miami, Florida, United States

Miami Cancer Institute at Bapt

Miami, Florida, United States

Inpatient Research Clinical LLC

Miami Lakes, Florida, United States

Inpatient Research Clinical LLC

Miami Lakes, Florida, United States

FXM Clin Res Miramar LLC

Miramar, Florida, United States

Ocala Cardiovascular Research

Ocala, Florida, United States

SEC Clinical Research

Pensacola, Florida, United States

Peace River Cardiovascular Center

Port Charlotte, Florida, United States

FC Site Partners Miami

Winter Park, Florida, United States

Advocate Lutheran General Childrens Hospital

Park Ridge, Illinois, United States

American Health Network Research Dept

Muncie, Indiana, United States

American Health Network Research Dept

Muncie, Indiana, United States

Cardiovascular Associates Research

Covington, Louisiana, United States

Omega Clinical Research

Metairie, Louisiana, United States

Anderson Medical Research

Ft. Washington, Maryland, United States

Henry Ford Hospital

Detroit, Michigan, United States

Aa Mrc Llc

Flint, Michigan, United States

MyMichigan Medical Center Midland

Midland, Michigan, United States

AB Clinical Trials

Las Vegas, Nevada, United States

Overlook Medical Center

Summit, New Jersey, United States

Wake Forest University Baptist Medical Center

Winston-Salem, North Carolina, United States

The Corvallis Clinic P C

Corvallis, Oregon, United States

Novartis Investigative Site

Tullahoma, Tennessee, United States

PharmaTex Research LLC

Amarillo, Texas, United States

Kelsey Seybold Research Foundation

Houston, Texas, United States

Northwest Houston Clinical Research PLLC

Tomball, Texas, United States

Intermountain Medical Center

Murray, Utah, United States

Virginia Heart

Falls Church, Virginia, United States

Novartis Investigative Site

Yinchuan, Ningxia, China

Novartis Investigative Site

Jining, Shandong, China

Novartis Investigative Site

Xian, Shanxi, China

Novartis Investigative Site

Beijing, China

Novartis Investigative Site

Shanghai, China

Novartis Investigative Site

Pessac, France

Novartis Investigative Site

Poitiers, France

Novartis Investigative Site

Stuttgart, Baden-Wurttemberg, Germany

Novartis Investigative Site

Potsdam, Brandenburg, Germany

Novartis Investigative Site

Berlin, Germany

Novartis Investigative Site

Bielefeld, Germany

Novartis Investigative Site

Gelnhausen, Germany

Novartis Investigative Site

Mannheim, Germany

Novartis Investigative Site

Münster, Germany

Novartis Investigative Site

Singen, Germany

Novartis Investigative Site

Hong Kong, Hong Kong, Hong Kong

Novartis Investigative Site

Hong Kong, Hong Kong

Novartis Investigative Site

Ancona, AN, Italy

Novartis Investigative Site

Caserta, CE, Italy

Novartis Investigative Site

Grosseto, GR, Italy

Novartis Investigative Site

Milan, MI, Italy

Novartis Investigative Site

Rozzano, MI, Italy

Novartis Investigative Site

The Hague, South Holland, Netherlands

Novartis Investigative Site

Enschede, Netherlands

Latin Clinical Trial Center Inc

San Juan, Puerto Rico

Novartis Investigative Site

Santiago Compostela, A Coruna, Spain

Novartis Investigative Site

Pamplona, Navarre, Spain

Novartis Investigative Site

Castilleja de la Cuesta, Sevilla, Spain

Novartis Investigative Site

A Coruña, Spain

Novartis Investigative Site

Barcelona, Spain

Novartis Investigative Site

Córdoba, Spain

Novartis Investigative Site

Huelva, Spain

Novartis Investigative Site

Las Palmas GC, Spain

Novartis Investigative Site

Salamanca, Spain

Novartis Investigative Site

Valencia, Spain

Novartis Investigative Site

Changhua, Taiwan

Novartis Investigative Site

Kaohsiung City, Taiwan

Novartis Investigative Site

Tainan, Taiwan

Novartis Investigative Site

Taipei, Taiwan

Novartis Investigative Site

Taipei, Taiwan

Novartis Investigative Site

Chichester, West Sussex, United Kingdom

Novartis Investigative Site

London, United Kingdom

Novartis Investigative Site

London, United Kingdom

Novartis Investigative Site

Manchester, United Kingdom

Novartis Investigative Site

Tyne and Wear, United Kingdom

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NCT06813911


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