RecruitingPhase 2Phase 3NCT06989437

A Study to Learn About the Medicine Ponsegromab in Adults With Cancer of the Pancreas Which Has Spread and Caused Significant Body Weight Loss and Fatigue

A Phase 2b/3, Randomized, Double-Blind Study to Investigate the Efficacy, Safety, and Tolerability of Ponsegromab (PF-06946860) Compared With Placebo Both With Background First-Line Chemotherapy in Adult Participants With Cachexia and Metastatic Pancreatic Ductal Adenocarcinoma


Sponsor

Pfizer

Enrollment

982 participants

Start Date

Oct 3, 2025

Study Type

INTERVENTIONAL

Conditions

Summary

Study to investigate the efficacy, safety and tolerability of systemic chemotherapy plus ponsegromab versus systemic chemotherapy plus placebo for the first-line treatment in adult participants with cachexia and metastatic pancreatic ductal adenocardinoma.


Eligibility

Min Age: 18 Years

Inclusion Criteria5

  • Signed Informed Consent Document
  • Documented active diagnosis of metastatic pancreatic ductal adenocarcinoma
  • Cachexia defined by Fearon criteria of weight loss
  • Completed 1 x 28-day cycle of first-line systemic nab-paclitaxel and gemcitabine chemotherapy or 2 x 14-day cycles of FOLFIRINOX chemotherapy and prior to receiving Cycle 2 chemotherapy
  • ECOG PS ≤1 with life expectancy of at least 4 months

Exclusion Criteria10

  • Current active reversible causes of decreased food intake
  • Cachexia caused by other reasons
  • Any prior or current clinical diagnosis of heart failure, irrespective of left ventricular ejection fraction or New York Heart Association classification
  • Left ventricular ejection fraction \<50%
  • Receiving tube feedings or parenteral nutrition at the time of Screening or Randomization
  • History of allergic or anaphylactic reaction to any therapeutic or diagnostic monoclonal antibody
  • History of allergy or hypersensitivity to any of the chemotherapeutics or any of their excipients
  • Neuroendocrine (carcinoid, islet cell) or acinar pancreatic carcinoma, symptomatic brain metastasis, leptomeningeal disease or other active CNS metastases
  • Inadequate liver function
  • Renal disease requiring dialysis or eGFR \<30 mL/min/1.73m2

Interventions

DRUGponsegromab

Double-Blind ponsegromab Treatment

DRUGplacebo

Double-Blind placebo Treatment


Locations(68)

Central Arkansas Radiation Therapy Institute, dba CARTI

Bryant, Arkansas, United States

Central Arkansas Radiation Therapy Institute, dba CARTI

Conway, Arkansas, United States

CARTI Cancer Center

Little Rock, Arkansas, United States

Central Arkansas Radiation Therapy Institute, dba CARTI

North Little Rock, Arkansas, United States

Central Arkansas Radiation Therapy Institute, dba CARTI

Pine Bluff, Arkansas, United States

Cedars-Sinai Cancer at Cedars-Sinai Medical Center

Los Angeles, California, United States

Providence Medical Foundation

Santa Rosa, California, United States

Invision, LLC

Honolulu, Hawaii, United States

University of Hawaii Cancer Center

Honolulu, Hawaii, United States

Cardiology Associates, Inc

‘Aiea, Hawaii, United States

Hope and Healing Cancer Services

Hinsdale, Illinois, United States

Hope and Healing Cancer Services New Lenox

New Lenox, Illinois, United States

Renown Health Medical Oncology

Reno, Nevada, United States

Renown Office of Clinical Research

Reno, Nevada, United States

Renown Regional Medical Center

Reno, Nevada, United States

OHSU Center for Health & Healing 1

Portland, Oregon, United States

Oregon Health and Science University

Portland, Oregon, United States

OSHU Center for Health and Healing 2

Portland, Oregon, United States

Virginia Mason Medical Center

Seattle, Washington, United States

Shoalhaven District Memorial Hospital

Nowra, New South Wales, Australia

ICON Cancer Centre - Kurralta Park

Kurralta Park, South Australia, Australia

Icon Cancer Centre Hobart

Hobart, Tasmania, Australia

Western Health-Sunshine & Footscray Hospitals

St Albans, Victoria, Australia

CIUSSS- saguenay-Lac-Saint-Jean

Chicoutimi, Quebec, Canada

Jewish General Hospital

Montreal, Quebec, Canada

Qilu Hospital of Shandong University

Jinan, Shandong, China

Ruijin Hospital Affiliated to Shanghai Jiao Tong University School of Medicine

Shanghai, Shanghai Municipality, China

Venkateshwar Hospital

New Delhi, National Capital Territory of Delhi, India

Rajiv Gandhi Cancer Institute And Research Centre

New Delhi, National Capital Territory of Delhi, India

Rabin Medical Center

Petah Tikva, Central District, Israel

Sheba Medical Center

Ramat Gan, Central District, Israel

Shaare Zedek Medical Center

Jerusalem, Jerusalem, Israel

Hadassah Medical Center

Jerusalem, Jerusalem, Israel

Rambam Health Care Campus

Haifa, Northern District, Israel

Sourasky Medical Center

Tel Aviv, TELL ABĪB, Israel

Chiba cancer center

Chiba, Chiba, Japan

National Cancer Center Hospital East

Kashiwa, Chiba, Japan

Kagawa University Hospital

Kita-gun, Kagawa-ken, Japan

St. Marianna University Hospital

Kawasaki, Kanagawa, Japan

Kanagawa cancer center

Yokohama, Kanagawa, Japan

The University of Osaka Hospital

Suita, Osaka, Japan

National Cancer Center Hospital

Chuo-ku, Tokyo, Japan

The Cancer Institute Hospital of JFCR

Koto-ku, Tokyo, Japan

Wakayama Minami Radiology Clinic

Wakayama-shi Kimiidera 870-2, Wakayama, Japan

Yamaguchi University Hospital

Ube, Yamaguchi, Japan

National Hospital Organization Kyushu Cancer Center

Fukuoka, Japan

Kyushu University Hospital

Fukuoka, Japan

University Hospital,Kyoto Prefectural University of Medicine

Kyoto, Japan

Wakayama Medical University Hospital

Wakayama, Japan

Pan American Center for Oncology Trials, LLC - Dorado Office

Dorado, Puerto Rico

Pan American Center for Oncology Trials, LLC - Mayaguez Office

Mayagüez, Puerto Rico

Pan American Center for Oncology Trials, LLC

Rio Piedras, Puerto Rico

Pan American Center for Oncology Trials, LLC

San Juan, Puerto Rico

Inha University Hospital

Incheon, Incheon-gwangyeoksi [incheon], South Korea

Seoul National University Bundang Hospital

Seongnam, Kyǒnggi-do, South Korea

CHA Bundang Medical Center, CHA University

Seongnam-si, Kyǒnggi-do, South Korea

Seoul National University Hospital

Seoul, Seoul-teukbyeolsi [seoul], South Korea

Severance Hospital, Yonsei University Health System

Seoul, Seoul-teukbyeolsi [seoul], South Korea

Asan Medical Center

Seoul, Seoul-teukbyeolsi [seoul], South Korea

Samsung Medical Center

Seoul, Seoul-teukbyeolsi [seoul], South Korea

The Catholic Univ. of Korea Seoul St. Mary's Hospital

Seoul, Seoul-teukbyeolsi [seoul], South Korea

Keimyung University Dongsan Hospital

Daegu, Taegu-kwangyǒkshi, South Korea

Inje University Haeundae Paik Hospital

Busan, South Korea

Kaohsiung Medical University Chung-Ho Memorial Hospital

Kaohsiung City, Taiwan

China Medical University Hospital

Taichung, Taiwan

National Cheng Kung University Hospital

Tainan, Taiwan

National Taiwan University Hospital

Taipei, Taiwan

Taipei Veterans General Hospital

Taipei, Taiwan

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NCT06989437


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