RecruitingPhase 2Phase 3NCT07129993

Study of Datopotamab Deruxtecan Plus Carboplatin or Cisplatin Versus Gemcitabine Plus Carboplatin or Cisplatin in Participants With Locally Advanced or Metastatic Urothelial Carcinoma

A Randomized, Open-Label, Phase 2/3 Study of Datopotamab Deruxtecan (Dato-DXd) Plus Carboplatin or Cisplatin Versus Gemcitabine Plus Carboplatin or Cisplatin in Participants With Locally Advanced or Metastatic Urothelial Carcinoma (la/mUC) Who Progressed During or After Enfortumab Vedotin (EV) Plus Pembrolizumab Combination Treatment TROPION-Urothelial03 (TU03)


Sponsor

Daiichi Sankyo

Enrollment

630 participants

Start Date

Sep 26, 2025

Study Type

INTERVENTIONAL

Conditions

Summary

This is a global, multicenter, randomized, open-label, Phase 2/3 study of Dato-DXd plus carboplatin or cisplatin versus gemcitabine plus carboplatin or cisplatin in participants with la/mUC who progressed during or after EV plus pembrolizumab combination treatment. This trial will start with part A, Phase 2. During part A, Phase 2, preliminary efficacy and safety will be assessed, and the recommended Phase 3 dose (RP3D) will be identified when the data allow sufficient assessment of activity, safety, and tolerability. The Phase 3 part will start contingent upon the assessment in the Phase 2 part, taking into consideration the totality of information.


Eligibility

Min Age: 18 Years

Plain Language Summary

Simplified for easier understanding

This study is comparing a new treatment combination (datopotamab deruxtecan plus platinum chemotherapy) against standard chemotherapy (gemcitabine plus platinum) in people with advanced bladder or urinary tract cancer. **You may be eligible if...** - You are 18 or older - You have been confirmed to have advanced or metastatic urothelial carcinoma (cancer of the bladder, ureter, renal pelvis, or urethra) - You have not received prior treatment for your advanced-stage cancer - Your overall health and organ function meet study requirements **You may NOT be eligible if...** - You have a rare type of bladder cancer (urachal, small cell, or adenocarcinoma) - You have previously received systemic therapy for your advanced cancer - You have brain metastases that are unstable - You have a history of serious lung inflammation (ILD/pneumonitis) - You have an active autoimmune disease requiring treatment Talk to your doctor to see if this trial is right for you.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

DRUGDato-DXd

Dato-DXd will be administered as an intravenous (IV) infusion every three weeks (Q3W) at a dose of 4 mg/kg or 6 mg/kg in Part A or RP3D in Part B

DRUGCarboplatin

Carboplatin will be administered as an intravenous (IV) infusion every three weeks (Q3W) at a dose of AUC 4.5 or 5.0 mg•min/mL

DRUGCisplatin

Cisplatin will be administered as an intravenous (IV) infusion every three weeks (Q3W) at a dose of 70 mg/m2

DRUGGemcitabine

Gemcitabine will be administered as an IV infusion at a dose of 1000 mg/m2 on Day 1 and 8 of every 3 week cycle.


Locations(79)

Research Site

Fullerton, California, United States

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La Jolla, California, United States

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San Francisco, California, United States

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Aurora, Colorado, United States

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Orange City, Florida, United States

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St. Petersburg, Florida, United States

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Tamarac, Florida, United States

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Atlanta, Georgia, United States

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Locust Grove, Georgia, United States

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Effingham, Illinois, United States

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Niles, Illinois, United States

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Peoria, Illinois, United States

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Largo, Maryland, United States

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Grand Rapids, Michigan, United States

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St Louis, Missouri, United States

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New York, New York, United States

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Raleigh, North Carolina, United States

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Portland, Oregon, United States

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Philadelphia, Pennsylvania, United States

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Myrtle Beach, South Carolina, United States

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Germantown, Tennessee, United States

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Nashville, Tennessee, United States

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Austin, Texas, United States

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Dallas, Texas, United States

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Dallas, Texas, United States

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Charlottesville, Virginia, United States

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Norfolk, Virginia, United States

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Spokane, Washington, United States

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Madison, Wisconsin, United States

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Krems, Austria

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Vienna, Austria

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Beijing, China

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Chengdu, China

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Guangzhou, China

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Angers, France

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Bordeaux, France

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Brest, France

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Calais, France

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Cedex 10, France

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Créteil, France

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Grenoble, France

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La Chaussée-Saint-Victor, France

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La Roche-sur-Yon, France

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Le Mans, France

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Lyon, France

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Marseille, France

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Montpellier, France

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Nantes, France

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Nîmes, France

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Paris, France

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Paris, France

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Pierre-Bénite, France

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Poitiers, France

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Quint-Fonsegrives, France

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Reims, France

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Saint-Etienne, France

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Saint-Herblain, France

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Toulouse, France

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Vandœuvre-lès-Nancy, France

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Nürtingen, Germany

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Naples, Italy

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Roma, Italy

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Rozzano, Italy

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Bunkyō City, Japan

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Bunkyō City, Japan

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Fukuoka, Japan

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Hirosaki-shi, Japan

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Kanazawa, Japan

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Kawasaki, Japan

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Kōtoku, Japan

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Kumamoto, Japan

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Nagoya, Japan

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Niigata, Japan

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Okayama, Japan

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Osaka, Japan

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Sapporo, Japan

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Shinjuku-ku, Japan

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Toyama, Japan

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Ube-shi, Japan

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NCT07129993


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