RecruitingPhase 3NCT07220083

A Study to Find Out if BI 764198 Helps Adults and Adolescents With a Kidney Condition Called Focal Segmental Glomerulosclerosis (FSGS)

A Multicentre, Randomised, Double-blind, Parallel Group, Placebo-controlled Trial to Assess the Effects of Oral TRPC6 Inhibitor BI 764198 Taken Over a 104 Week Treatment Period in Adult and Adolescent Participants With Primary Focal Segmental Glomerulosclerosis (pFSGS) or Genetic FSGS Related to TRPC6 Gene Variants


Sponsor

Boehringer Ingelheim

Enrollment

286 participants

Start Date

Feb 16, 2026

Study Type

INTERVENTIONAL

Conditions

Summary

This study is open to adults and adolescents with a kidney condition called focal segmental glomerulosclerosis (FSGS). The purpose of this study is to find out whether a medicine called BI 764198 helps people with FSGS. Participants are put into 2 groups randomly, which means by chance. Every participant has an equal chance of being in each group. One group takes BI 764198 tablets, and the other group takes placebo tablets. Placebo tablets look like BI 764198 tablets but do not contain any medicine. Participants take a tablet once a day for up to 2 years. All participants also continue their standard medication for FSGS. Participants are in the study for up to 2 years. During this time, they visit the study site about every 3 months. Participants regularly collect urine samples. This is done to check their kidneys. The results are compared between the two groups to see whether the treatment works. The doctors also regularly check participants' health and take note of any unwanted effects.


Eligibility

Min Age: 12 Years

Inclusion Criteria9

  • Male or female participants ≥12 years old on the day of signing informed consent/assent (Visit 1)
  • Weight of ≥40 kg at the screening visit (Visit 1)
  • Body mass index (BMI) of ≤40 kg/m² at the screening visit (Visit 1)
  • Participants with a diagnosis prior to the screening visit (Visit 1) of either:
  • Biopsy-confirmed primary focal segmental glomerulosclerosis (pFSGS) (based on Investigator's judgement) OR
  • Genetic focal segmental glomerulosclerosis (FSGS) resulting from a gain-of-function mutation in the transient receptor potential cation subfamily C member 6 (TRPC6) gene (based on historical genetic test)
  • Urine protein-creatinine ratio (UPCR) ≥1500 mg/g based on the mean of the spot urine sample and first morning void urine sample (both assessed by central laboratory) at the screening visit (Visit 1)
  • Estimated glomerular filtration rate (eGFR)
  • For adult participants (≥18 years): ≥25 mL/min/1.73 m² (chronic kidney disease epidemiology collaboration (CKD-EPI) formula based on combined serum creatinine plus cystatin C) at the screening visit (Visit 1)

Exclusion Criteria4

  • Known monogenic or syndromic causes of FSGS (with the exception of TRPC6 gain-of-function gene mutations)
  • Clinical or histologic evidence of secondary maladaptive or toxic forms of FSGS (based on Investigator's judgement)
  • FSGS of undetermined cause (FSGS-UC) with a diagnosis prior to the screening visit (Visit 1) (based on Investigator's judgement)
  • A history of organ transplantation or planned organ transplantation during the course of the trial

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Interventions

DRUGBI 764198

BI 764198

DRUGPlacebo

Placebo matching BI 764198


Locations(251)

Alabama Kidney Research

Alabaster, Alabama, United States

Apogee Clinical Research

Huntsville, Alabama, United States

Southwest Kidney Institute

Surprise, Arizona, United States

West Coast Kidney Institute

Fremont, California, United States

Kidney Disease Medical Group

Glendale, California, United States

Amicis Research Center - Balboa

Granada Hills, California, United States

Valiance Clinical Research

Huntington Park, California, United States

Academic Medical Research Institute - Glendale

Los Angeles, California, United States

University of California Los Angeles

Los Angeles, California, United States

North America Research Institute

San Dimas, California, United States

Kaiser Permanente - French Campus

San Francisco, California, United States

Valiance Clinical Research-Tarzana-68237

Tarzana, California, United States

National Institute of Clinical Research - Victorville

Victorville, California, United States

Kidney Associates of Colorado - Denver

Denver, Colorado, United States

Colorado Kidney Center

Denver, Colorado, United States

Florida Kidney Physicians - Boca Raton

Boca Raton, Florida, United States

Florida Kidney Physicians, LLC - Fort Lauderdale

Fort Lauderdale, Florida, United States

Total Research Group, LLC

Miami, Florida, United States

CTR Oakwater, LLC

Orlando, Florida, United States

Panoramic Health

Riverview, Florida, United States

Emory Children's Center

Atlanta, Georgia, United States

Southeast Kidney Associates - East Point

East Point, Georgia, United States

Memorial Health University Hospital

Savannah, Georgia, United States

Ann & Robert H. Lurie Children's Hospital of Chicago

Chicago, Illinois, United States

Northwestern University

Chicago, Illinois, United States

Endeavor Health

Evanston, Illinois, United States

Wichita Nephrology Group

Wichita, Kansas, United States

Northwest Louisiana Nephrology

Shreveport, Louisiana, United States

Johns Hopkins Hospital

Baltimore, Maryland, United States

Joslin Diabetes Center

Boston, Massachusetts, United States

Henry Ford Hospital

Detroit, Michigan, United States

St. Clair Nephrology Research, LLC - Shelby Township

Utica, Michigan, United States

Mayo Clinic, Rochester

Rochester, Minnesota, United States

Elixia MNA, LLC

City of Saint Peters, Missouri, United States

DaVita Clinical Research-Las Vegas-67781

Las Vegas, Nevada, United States

New York Nephrology and Dialysis Access Surgery, PC

Clifton Park, New York, United States

NYU Langone Nephrology Associates-Mineola

Mineola, New York, United States

Duke University Medical Center

Durham, North Carolina, United States

The Kidney and Hypertension Center

Cincinnati, Ohio, United States

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States

Nationwide Children's Hospital

Columbus, Ohio, United States

The Ohio State University Wexner Medical Center

Columbus, Ohio, United States

Northeast Clinical Research Center

Bethlehem, Pennsylvania, United States

Clinical Renal Associates

Exton, Pennsylvania, United States

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Nephrology Associates, Inc

East Providence, Rhode Island, United States

Southeast Renal Research Institute

Chattanooga, Tennessee, United States

Texas Tech University Health Sciences Center-Amarillo-63885

Amarillo, Texas, United States

Research Management, Inc - Austin

Austin, Texas, United States

Nephrotex Research Group

Dallas, Texas, United States

University of Texas Medical Branch at Galveston

Galveston, Texas, United States

Provecta Researh Network

Houston, Texas, United States

Utah Kidney Research Institute

Salt Lake City, Utah, United States

Virginia Nephrology

Arlington, Virginia, United States

Virginia Commonwealth University

Richmond, Virginia, United States

West Virginia University Medicine

Morgantown, West Virginia, United States

Terapia Renal Domiciliaria

Buenos Aires, Argentina

Hospital Italiano de Buenos Aires

CABA, Argentina

CEMIC

CABA, Argentina

Centro Medico Dra Laura Maffei

Ciudad Autonoma Buenos Aires, Argentina

Clinica Privada Velez Sarfield

Córdoba, Argentina

Hospital Universitario Austral

Pilar, Argentina

CardioAlem Investigaciones

San Isidro, Argentina

Nepean Hospital

Kingswood, New South Wales, Australia

St George Hospital

Kogarah, New South Wales, Australia

Royal Brisbane and Women's Hospital

Herston, Queensland, Australia

Griffith Health

Southport, Queensland, Australia

Royal Adelaide Hospital

Adelaide, South Australia, Australia

Royal Melbourne Hospital

Parkville, Victoria, Australia

AZORG Ziekenhuis

Aalst, Belgium

UZ Leuven

Leuven, Belgium

Centre Hospitalier Universitaire de Liège

Liège, Belgium

Synvia

Campinas, Brazil

Universidade Federal do Ceará

Fortaleza, Brazil

Hospital de Clínicas de Porto Alegre

Porto Alegre, Brazil

Hospital das Clínicas da Universidade Federal de Pernambuco

Recife, Brazil

Fundação Oswaldo Ramos (Hospital do Rim)

São Paulo, Brazil

Centro de Pesquisa Clínica de Nefrologia do ICHC

São Paulo, Brazil

Instituto da Criança e do Adolescente

São Paulo, Brazil

Victoria Hospital (LHSC)

London, Ontario, Canada

Maisonneuve-Rosemont Hospital

Montreal, Quebec, Canada

The First Affiliated Hospital of Baotou Medical College

Baotou, China

Peking University First Hospital

Beijing, China

Beijing Tsinghua Changgung Hospital

Beijing, China

The Second Hospital of Jilin University

Changchun, China

The Second Xiangya Hospital Of Central South University

Changsha, China

West China Hospital, Sichuan University

Chengdu, China

People's Hospital of Sichuan Province

Chengdu, China

Guangdong Provincial People's Hospital

Guangzhou, China

Guizhou People's Hospital

Guiyang, China

The First Affiliated Hospital, Zhejiang University

Hangzhou, China

Lanzhou University Second Hospital

Lanzhou, China

The First Affiliated Hospital of Nanchang University

Nanchang, China

Zhongda Hospital Southeast University

Nanjing, China

The First People's Hospital of Nanning

Nanning, China

The First Affiliated Hospital of Guangxi Medical University

Nanning, China

Ruijin Hospital, Shanghai Jiao Tong University School of Medicine

Shanghai, China

Huashan Hospital, Fudan University

Shanghai, China

Shanghai General Hospital

Shanghai, China

Shanxi Provincial People's Hospital

Taiyuan, China

Renmin Hospital of Wuhan University

Wuhan, China

First Affiliated Hospital of Xi'an JiaoTong University

Xi'an, China

Zhongshan Hospital Affiliated to Xiamen University

Xiamen, China

Clinical Hospital Sveti Duh

Zagreb, Croatia

Poliklinika Bonifarm Zagreb

Zagreb, Croatia

Copenhagen University Hospital, Rigshospitalet

København Ø, Denmark

Zealand University Hospita; Roskilde

Roskilde, Denmark

CHU Amiens-Picardie

Amiens, France

HOP Pellegrin

Bordeaux, France

HOP de la Cavale Blanche

Brest, France

Hôpital Henri Mondor

Créteil, France

Hôpital Edouard Herriot

Lyon, France

Hôpital Pasteur

Nice, France

CHU de Nîmes

Nîmes, France

Hôpital Necker

Paris, France

HOP Nancy

Vandœuvre-lès-Nancy, France

LTD Israeli-Georgian Medical Research Clinic Healthycore

Tbilisi, Georgia

LEPL The First University Clinic of Tbilisi State Medical University

Tbilisi, Georgia

M.Iashvili Children's Hospital

Tbilisi, Georgia

Vivantes Klinikum im Friedrichshain

Berlin, Germany

Universitätsklinikum Köln (AöR)

Cologne, Germany

Universitätsklinikum Hamburg, Eppendorf

Hamburg, Germany

Medizinische Hochschule Hannover

Hanover, Germany

Universitätsklinikum Heidelberg

Heidelberg, Germany

Universität Leipzig

Leipzig, Germany

Universitätsmedizin der Johannes Gutenberg-Universität Mainz

Mainz, Germany

Universitätsklinikum Würzburg AÖR

Würzburg, Germany

University General Hospital of Heraklion

Heraklion, Greece

Univ. Gen. Hosp. of Patras

Pátrai, Greece

Hong Kong Children's Hospital

Hong Kong, Hong Kong

Queen Mary Hospital

Hong Kong, Hong Kong

Aartham Multi Super Speciality Hospital

Ahmedabad, India

AIIMS Bhubaneshwar

Bhubaneswar, India

Government Medical College

Kozhikode, India

Noble Hospital Pvt Ltd

Pune, India

Galaxy Lifecare Services Pvt. Ltd.

Varanasi, India

Azienda Universitaria Ospedaliera Consorziale Policlinico Bari

Bari, Italy

Policlinico S. Orsola-Malpighi

Bologna, Italy

Asst Santi Paolo E Carlo

Milan, Italy

Azienda Ospedaliera Universitaria Policlinico Paolo Giaccone

Palermo, Italy

Fondazione Salvatore Maugeri

Pavia, Italy

ASST dei Sette Laghi

Varese, Italy

Kasugai Municipal Hospital

Aichi, Kasugai, Japan

Daido Clinic

Aichi, Nagoya, Japan

Japanese Red Cross Aichi Medical Center Nagoya Daini Hospital

Aichi, Nagoya, Japan

Chiba University Hospital

Chiba, Chiba, Japan

National Hospital Organization Chibahigashi National Hospital

Chiba, Chiba, Japan

Japanese Red Cross Fukuoka Hospital

Fukuoka, Fukuoka, Japan

Kurume University Hospital

Fukuoka, Kurume, Japan

Kobe University Hospital

Hyogo, Kobe, Japan

Saiseikai Yokohamashi Nanbu Hospital

Kanagawa, Yokohama, Japan

Yokohama City University Hospital

Kanagawa, Yokohama, Japan

Nara Prefecture General Medical Center

Nara, Nara, Japan

Niigata University Medical and Dental Hospital

Niigata, Niigata, Japan

Okayama University Hospital

Okayama, Okayama, Japan

Dokkyo Medical University Saitama Medical Center

Saitama, Koshigaya, Japan

Institute of Science Tokyo Hospital

Tokyo, Bunkyo-ku, Japan

Tokyo Medical University Hachioji Medical Center

Tokyo, Hachioji, Japan

The Jikei University Hospital

Tokyo, Minato-ku, Japan

Tokyo Women's Medical University Hospital

Tokyo, Shinjuku-ku, Japan

Hospital Sultan Idris Shah Serdang

Kajang, Malaysia

Queen Elizabeth Hospital

Kota Kinabalu, Malaysia

Hospital Kuala Lumpur

Kuala Lumpur, Malaysia

University Malaya Medical Centre

Lembah Pantai, Malaysia

Hospital Tuanku Ja'afar

Negeri Sembilan, Malaysia

Sunway Medical Centre

Subang Jaya, Malaysia

Centenario Hospital Miguel Hidalgo

Aguascalientes, Mexico

Health Pharma Professional Research S.A. de C.V.

Mexico City, Mexico

Soltmed Smo

Mexico City, Mexico

Instituto Nacional de Cardiologia Ignacio Chavez

Mexico City, Mexico

Instituto Nacional de Cs Médicas y Nutrición S Zubiran

Mexico City, Mexico

Servicios de Oncología Médica Integral, S.A. de C.V. Sucursal Renal

Monterrey, Mexico

Amsterdam UMC Locatie AMC

Amsterdam, Netherlands

Universitair Medisch Centrum Groningen

Groningen, Netherlands

Radboud Universitair Medisch Centrum

Nijmegen, Netherlands

Waikato Hospital

Hamilton, Waikato Region, New Zealand

Optimal Clinical Trials - Christchurch

Christchurch, New Zealand

Taranaki Base Hospital

New Plymouth, New Zealand

Optimal Clinical Trials North

Rosedale, Auckland, New Zealand

Akershus Universitetssykehus HF

Lørenskog, Norway

Oslo Universitetssykehus HF, Ullevål sykehus

Oslo, Norway

Helse Stavanger, Stavanger Universitetssykehus

Stavanger, Norway

Universitetssykehuset Nord-Norge, Tromsø

Tromsø, Norway

Manila Doctors Hospital

Manila, Philippines

Centralny Szpital Kliniczny Uniwersytetu Medycznego w Łodzi

Lodz, Poland

Uniwersytet Medyczny im. Karola Marcinkowskiego w Poznaniu

Poznan, Poland

Pomorski Uniwersytet Medyczny w Szczecinie, Samodzielny Publiczny Szpital Kliniczny nr 2

Szczecin, Poland

Samodzielny Publiczny Dzieciecy Szpital Kliniczny Im. Jozefa Polikarpa Brudzinskiego W Warszawie

Warsaw, Poland

Centralny Szpital Kliniczny MON WIM

Warsaw, Poland

ULS de Almada -Seixal, E. P. E. - Hospital Garcia de Orta

Almada, Portugal

ULS de Amadora/ Sintra, E.P.E. - Hospital Professor Doutor Fernando Fonseca

Amadora, Portugal

ULS Braga

Braga, Portugal

CHUC - Centro Hospitalar e Universitário de Coimbra, EPE

Coimbra, Portugal

ULS de São José

Lisbon, Portugal

ULS de Santa Maria, E.P.E

Lisbon, Portugal

Unidade Local de Saúde Lisboa Occidental, E.P.E

Lisbon, Portugal

ULS de Loures-Odivelas, E.P.E

Loures, Portugal

ULS de Santo Antônio, E.P.E - Centro Hospitalar Universitário de Santo António

Porto, Portugal

Unidade Local de Saúde da Arrábida,E.P.E

Setúbal, Portugal

Institutul Clinic Fundeni

Bucharest, Romania

Spitalul Clinic Judetean de urgenta Cluj

Cluj-Napoca, Romania

National University Hospital

Singapore, Singapore

Singapore General Hospital

Singapore, Singapore

Tan Tock Seng Hospital

Singapore, Singapore

Faculty hospital with clinics F.D. Roosevelta

Banská Bystrica, Slovakia

University Hospital and Comenius University in Bratislava, Derer´s Hospital

Bratislava, Slovakia

Univerzitna nemocnica L. Pasteura Kosice

Košice, Slovakia

Univ. Hospital Martin

Martin, Slovakia

Pusan National University Hospital

Busan, South Korea

Samsung Medical Center

Gangnam-gu, South Korea

Inje University Ilsan Paik Hospital

Goyang, South Korea

Severance Hospital

Seoul, South Korea

Kyung Hee University Hospital at Gangdong

Seoul, South Korea

Ajou University Hospital

Suwon, South Korea

Complejo Hospitalario Torrecárdenas

Almería, Spain

Hospital del Mar

Barcelona, Spain

Hospital Universitari Vall d'Hebron

Barcelona, Spain

Hospital Clínic de Barcelona

Barcelona, Spain

Hospital Sant Joan de Déu

Barcelona, Spain

Hospital Universitario Virgen de las Nieves

Granada, Spain

Hospital Clínico San Carlos

Madrid, Spain

Hospital Universitario 12 de Octubre

Madrid, Spain

Danderyds Sjukhus

Danderyd, Sweden

Universitetssjukhuset, Linköping

Linköping, Sweden

Skånes universitetssjukhus

Lund, Sweden

Karolinska Universitetssjukhuset

Stockholm, Sweden

Uppsala University Hospital

Uppsala, Sweden

University Hospital Bern

Bern, Switzerland

University Hospital Zurich

Zurich, Switzerland

Buddhist Tzu Chi General Hospital-Hualien-20741

Hualien City, Taiwan

Kaohsiung Chang Gung Memorial Hospital

Kaohsiung City, Taiwan

Far Eastern Memorial Hospital

New Taipei City, Taiwan

Taipei Medical University-Shuang Ho Hospital

New Taipei City, Taiwan

China Medical University Hospital

Taichung, Taiwan

Taichung Veterans General Hospital

Taichung, Taiwan

National Cheng Kung University Hospital

Tainan, Taiwan

National Taiwan University Hospital

Taipei, Taiwan

Chang Gung Memorial Hospital, Linkou

Taoyuan, Taiwan

Adana City Hospital

Adana, Turkey (Türkiye)

Ankara Etlik City Hospital

Ankara, Turkey (Türkiye)

Bursa Uludag University

Bursa, Turkey (Türkiye)

İstanbul Çapa University

Istanbul, Turkey (Türkiye)

Kocaeli University Faculty of Medicine Hospital

İzmit, Turkey (Türkiye)

Erciyes University

Melikgazi/Kayseri, Turkey (Türkiye)

Clatterbridge Hospital

Bebington, United Kingdom

Bradford Institute for Health Research

Bradford, United Kingdom

Addenbrooke's Hospital

Cambridge, United Kingdom

Leicester General Hospital

Leicester, United Kingdom

Royal Free Hospital

London, United Kingdom

King's College Hospital

London, United Kingdom

Salford Royal

Salford, United Kingdom

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NCT07220083


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