RecruitingNCT07223489
Diagnostic Journey, Patient Experience, and Disparities in the Treatment of Spinal Muscular Atrophy (SMA) in the MedStar Health System
Understanding the Diagnostic Pathway and Treatment Experience of Patients With Spinal Muscular Atrophy (SMA)
Sponsor
Medstar Health Research Institute
Enrollment
200 participants
Start Date
Oct 10, 2025
Study Type
OBSERVATIONAL
Conditions
Summary
Evaluate the diagnostic journey, patient experience, and disparities in the treatment of Spinal Muscular Atrophy (SMA) in the MedStar Health System.
Eligibility
Min Age: 18 Years
Inclusion Criteria1
- SMA diagnosis, age greater than or equal to 18 years
Exclusion Criteria1
- Deceased
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Interventions
BEHAVIORALTelephone Interview
Telephone interviews to gather qualitative data on SMA patients' diagnostic journey, access to treatment and barriers encountered, understanding of their disease, and quality of life measures
Locations(1)
View Full Details on ClinicalTrials.gov
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NCT07223489
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