RecruitingNCT07356557

Evaluation of Therapeutic Adherence Among Patients Followed in the Department of Hereditary Metabolic Diseases at Necker Hospital


Sponsor

Assistance Publique - Hôpitaux de Paris

Enrollment

200 participants

Start Date

Feb 23, 2026

Study Type

OBSERVATIONAL

Conditions

Summary

The purpose of this study is to evaluate treatment adherence among patients followed in the Department of Inherited Metabolic Diseases at Necker Hospital, in order to assess the need for implementing a therapeutic education workshop focused on medication adherence.


Eligibility

Min Age: 7 YearsMax Age: 20 Years

Plain Language Summary

Simplified for easier understanding

This clinical trial is studying Calculation of the metabolic balance score and Questionnaire for people with metabolic diseases. The study is currently recruiting participants at 1 location. People eligible for this study include aged 7 Years to 20 Years.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

OTHERQuestionnaire

A pseudonymized questionnaire assessing treatment adherence, understanding of the illness, knowledge of medications, and the number of oral medications taken is given to patients and/or their parents during a follow-up visit, whether in a consultation, day hospital, or conventional hospitalization. It is completed by parents and children aged 7 and older, as well as by adolescents and young adults. The responses will not be disclosed to the physicians in the department.

OTHERCalculation of the metabolic balance score

For patients with urea cycle deficiency, a metabolic balance score will be calculated independently from retrospective data from the medical record, in the last two years preceding the completion of the questionnaire.


Locations(1)

Hôpital Necker-Enfants Malades

Paris, France

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NCT07356557


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