RecruitingPhase 1Phase 2NCT07531745

ASCEND: Safety and Tolerability of ION337 for the Treatment of Dravet Syndrome

Phase 1-2, Open-Label, Single and Multiple Ascending Dose Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Intrathecally-Administered ION337 in Patients With Dravet Syndrome


Sponsor

Ionis Pharmaceuticals, Inc.

Enrollment

32 participants

Start Date

May 21, 2026

Study Type

INTERVENTIONAL

Conditions

Summary

The primary purpose of this study is to evaluate the safety and tolerability of ION337 in participants with Dravet syndrome (DS).


Eligibility

Min Age: 2 YearsMax Age: 12 Years

Plain Language Summary

Simplified for easier understanding

This clinical trial is studying a drug called ION337 for people with dravet syndrome. The study is currently recruiting participants at 3 locations. People eligible for this study include aged 2 Years to 12 Years.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

DRUGION337

ION337 will be administered by ITB injection.


Locations(3)

University of Michigan Health System

Ann Arbor, Michigan, United States

Mayo Clinic

Rochester, Minnesota, United States

Le Bonheur Children's Hospital

Memphis, Tennessee, United States

View Full Details on ClinicalTrials.gov

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NCT07531745


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