RecruitingPhase 2NCT07608354

A Study to Evaluate the Efficacy and Safety of Concomitant Use of Eplontersen and ALXN2220 Compared With Eplontersen and Placebo for Adults Participants With ATTR-CM

A Phase IIb, Randomised, Double-blind, Placebo-controlled, Multicentre Study to Evaluate the Efficacy and Safety of Concomitant Use of Eplontersen and ALXN2220 Compared With Eplontersen and Placebo in Adult Participants With Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR-CM)


Sponsor

AstraZeneca

Enrollment

326 participants

Start Date

Jun 11, 2026

Study Type

INTERVENTIONAL

Conditions

Summary

The purpose of this randomised, double-blind, placebo-controlled, multicenter study is to evaluate the efficacy and safety of concomitant use of eplontersen and ALXN2220 compared with eplontersen and placebo in adult participants with Transthyretin-mediated amyloid cardiomyopathy (ATTR-CM).


Eligibility

Min Age: 18 YearsMax Age: 85 Years

Plain Language Summary

Simplified for easier understanding

This clinical trial is studying a biological treatment called ALXN2220, a drug called Eplontersen, and others for people with transthyretin amyloid cardiomyopathy (attr cm). The study is currently recruiting participants at 78 locations. People eligible for this study include aged 18 Years to 85 Years.

This summary was AI-generated to explain the trial in plain language. It is not medical advice. Always discuss eligibility with your doctor before enrolling in a clinical trial.

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Interventions

DRUGEplontersen

Eplontersen delivered subcutaneously, once every 4 weeks

BIOLOGICALALXN2220

ALXN2220 delivered intravenously, once every 4 weeks

OTHERPlacebo

Placebo delivered intravenously, once every 4 weeks


Locations(78)

Research Site

La Jolla, California, United States

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San Francisco, California, United States

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Stanford, California, United States

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Aurora, Colorado, United States

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Washington D.C., District of Columbia, United States

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Jacksonville, Florida, United States

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Miami, Florida, United States

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Weston, Florida, United States

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Chicago, Illinois, United States

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Boston, Massachusetts, United States

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Kansas City, Missouri, United States

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St Louis, Missouri, United States

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New York, New York, United States

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Chapel Hill, North Carolina, United States

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Durham, North Carolina, United States

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Cleveland, Ohio, United States

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Portland, Oregon, United States

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Danville, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Germantown, Tennessee, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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Salt Lake City, Utah, United States

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Falls Church, Virginia, United States

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Calgary, Alberta, Canada

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Vancouver, British Columbia, Canada

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Halifax, Nova Scotia, Canada

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London, Ontario, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Beijing, China

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Beijing, China

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Changsha, China

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Chongqing, China

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Guangzhou, China

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Hangzhou, China

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Créteil, France

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Marseille, France

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Rennes, France

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Toulouse, France

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Bad Krozingen, Germany

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Berlin, Germany

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Cologne, Germany

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Essen, Germany

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Hamburg, Germany

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Heidelberg, Germany

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Homburg, Germany

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München, Germany

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Münster, Germany

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Bologna, Italy

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Florence, Italy

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Milan, Italy

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Padova, Italy

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Pavia, Italy

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Pisa, Italy

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Torino, Italy

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Torrette - Ancona, Italy

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Trieste, Italy

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Bunkyō City, Japan

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Kurume-shi, Japan

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Sapporo, Japan

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Shinjuku-ku, Japan

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Suita, Japan

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Barcelona, Spain

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Jaén, Spain

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L'Hospitalet de Llobregat, Spain

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Majadahonda, Spain

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Málaga, Spain

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Pamplona, Spain

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Salamanca, Spain

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Valencia, Spain

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Gothenburg, Sweden

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Lund, Sweden

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Stockholm, Sweden

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Umeå, Sweden

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Uppsala, Sweden

Research Site

London, United Kingdom

Research Site

London, United Kingdom

View Full Details on ClinicalTrials.gov

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