AMI Clinical Trials in New York, New York
25 recruitingNew York, New York
Showing 1–20 of 25 trials
Recruiting
Phase 3
A Phase 3 Study of Zodasiran in Adolescent and Adult Subjects With Homozygous Familial Hypercholesterolemia (YOSEMITE)
Homozygous Familial Hypercholesterolemia
Arrowhead Pharmaceuticals60 enrolled35 locationsNCT07037771
Recruiting
Not Applicable
HealthySteps + PlayReadVIP
Families With Infants
NYU Langone Health1,000 enrolled1 locationNCT06941337
Recruiting
Phase 2
A Study of Lower Radiotherapy Dose to Treat Children With CNS Germinoma
GerminomaBasal Ganglia GerminomaDiabetes Insipidus+3 more
Children's Oncology Group240 enrolled109 locationsNCT06368817
Recruiting
Phase 3
A Study to Test Whether Nerandomilast Can Help Slow Down Changes in the Lung in People With a Family History of Pulmonary Fibrosis
Interstitial Lung DiseasesFamilial Pulmonary FibrosisInterstitial Lung Abnormalities
Boehringer Ingelheim80 enrolled56 locationsNCT07201922
Recruiting
International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry
Gaucher DiseaseCerebroside Lipidosis SyndromeGlucocerebrosidase Deficiency Disease+1 more
Genzyme, a Sanofi Company12,000 enrolled318 locationsNCT00358943
Recruiting
The Rogosin Institute Homozygous Familial Hypercholesterolemia Repository
Homozygous Familial Hypercholesterolemia
The Rogosin Institute60 enrolled1 locationNCT01109368
Recruiting
Phase 2
Ketamine for Methamphetamine Use Disorder
methamphetamine abuseSubstance Use DisordersSubstance Use
University of Texas Southwestern Medical Center120 enrolled5 locationsNCT06496750
Recruiting
Phase 1
A Study of Avutometinib for People With Solid Tumor Cancers
Solid TumorSolid Tumor, AdultNeuroblastoma+12 more
Memorial Sloan Kettering Cancer Center23 enrolled2 locationsNCT06104488
Recruiting
Phase 2Phase 3
A Study of a Potential Disease Modifying Treatment in Individuals at Risk for or With a Type of Early Onset AD Caused by a Genetic Mutation
DementiaAlzheimers DiseaseAlzheimers Disease, Familial
Washington University School of Medicine280 enrolled35 locationsNCT06647498
Recruiting
Phase 2Phase 3
A Study of Potential Disease Modifying Treatments in Individuals at Risk for or With a Type of Early Onset AD Caused by a Genetic Mutation
DementiaAlzheimers DiseaseAlzheimers Disease, Familial
Washington University School of Medicine280 enrolled35 locationsNCT05552157
Recruiting
Phase 3
A Trial of Setmelanotide in Patients With Congenital Hypothalamic Obesity (Sub-study of NCT05774756)
Hypothalamic ObesityMultiple Pituitary Hormone Deficiency Genetic FormSepto-Optic Dysplasia+3 more
Rhythm Pharmaceuticals, Inc.39 enrolled11 locationsNCT06760546
Recruiting
Pancreas Registry and High Risk Registry
Pancreas CancerPancreatitisChronic Pancreatitis+3 more
Icahn School of Medicine at Mount Sinai1,368 enrolled2 locationsNCT02775461
Recruiting
Not Applicable
Opioid Dispenser for Microdiscectomy/Laminectomy
Opioid UsePain, PostoperativeMEDICAL DEVICE+2 more
Hospital for Special Surgery, New York30 enrolled1 locationNCT06358040
Recruiting
Phase 3
Study to Evaluate Efficacy and Safety of Inclisiran in Children With Heterozygous Familial Hypercholesterolemia
Familial Hypercholesterolemia - Heterozygous
Novartis Pharmaceuticals51 enrolled66 locationsNCT06597019
Recruiting
The Natural History of Familial Dysautonomia
Familial Dysautonomia (Riley-Day Syndrome)Hereditary Sensory and Autonomic NeuropathiesHereditary Sensory and Autonomic Neuropathy 3
NYU Langone Health400 enrolled2 locationsNCT03920774
Recruiting
International Rare Histiocytic Disorders Registry (IRHDR)
Rare Histiocytic Disorders (RHDs)Erdheim-Chester Disease (ECD)Rosai-Dorfman Disease (RDD)+7 more
The Hospital for Sick Children400 enrolled15 locationsNCT02285582
Recruiting
Subclinical Transthyretin Cardiac Amyloidosis in V122I TTR Carriers
Amyloidosis CardiacAmyloidosis, HereditaryAmyloidosis, Familial+2 more
University of Texas Southwestern Medical Center500 enrolled3 locationsNCT05489549
Recruiting
Not Applicable
Phase II: Scalable Digital Delivery of CRAFT Training for Professionals to Maximize Treatment Rates of OUD in Families
Substance-Related DisordersFamily HealthCommunity Reinforcement And Family Training
We The Village, Inc.240 enrolled1 locationNCT06685003
Recruiting
LOWER: Lomitapide Observational Worldwide Evaluation Registry
Homozygous Familial Hypercholesterolemia
Amryt Pharma300 enrolled75 locationsNCT02135705
Recruiting
Longitudinal Study of Urea Cycle Disorders
Brain Diseases, Metabolic, InbornAmino Acid Metabolism, Inborn ErrorsUrea Cycle Disorders
Andrea Gropman1,500 enrolled15 locationsNCT00237315