Congenital Clinical Trials in Paris
23 recruitingParis, France
Showing 1–20 of 23 trials
Recruiting
Phase 2Phase 3
A Study in Pediatric Participants With Congenital Adrenal Hyperplasia (Balance-CAH)
Congenital Adrenal HyperplasiaClassic Congenital Adrenal Hyperplasia
Crinetics Pharmaceuticals Inc.153 enrolled32 locationsNCT07159841
Recruiting
Phase 1
A Phase 1b Study to Investigate Safety and Tolerability of ARGX-119 in Adult Participants With DOK7-Congenital Myasthenic Syndromes (CMS)
Congenital Myasthenic SyndromeCMS
argenx16 enrolled9 locationsNCT06436742
Recruiting
Natural History in Children up to 16 Years With Mild to Profound Hearing Loss Due to Mutations in GJB2 / OTOF Genes
OTOF Gene MutationDFNB9Congenital Deafness+4 more
Sensorion180 enrolled1 locationNCT05402813
Recruiting
Not Applicable
Respiratory Muscles and Work of Breathing in Children
Lung DiseasesNeuromuscular DiseasesScoliosis+4 more
Assistance Publique - Hôpitaux de Paris550 enrolled1 locationNCT05051254
Recruiting
Respiratory and Psychological Impact of Elective Surgery of Congenital Lung Malformations
Congenital Lung Malformations
Assistance Publique - Hôpitaux de Paris434 enrolled1 locationNCT06424392
Recruiting
Observational Study to Evaluate Long-Term Outcome in Hip Arthroplasty
Hip ReplacementFemur Head NecrosisPrimary, Secondary or Post-traumatic Osteoarthrosis+2 more
Corin2,500 enrolled13 locationsNCT02230826
Recruiting
Phase 3
Study to Evaluate Sepofarsen in Subjects With Leber Congenital Amaurosis (LCA) Type 10 (HYPERION)
Sensation DisordersLeber Congenital AmaurosisBlindness+3 more
Laboratoires Thea32 enrolled14 locationsNCT06891443
Recruiting
Phase 1Phase 2
A Trial of Lu AG13909 in Participants With Congenital Adrenal Hyperplasia
Congenital Adrenal Hyperplasia
H. Lundbeck A/S42 enrolled17 locationsNCT05669950
Recruiting
Phase 2
A Study to Evaluate Tabelecleucel in Participants With Epstein Barr Virus (EBV) Associated Diseases
LeiomyosarcomaSolid Organ Transplant ComplicationsLymphoproliferative Disorders+8 more
Pierre Fabre Medicament190 enrolled40 locationsNCT04554914
Recruiting
Prenatal Maternal Mental Health and Neurodevelopment in Congenital Heart Disease
Congenital Heart Disease
Institut National de la Santé Et de la Recherche Médicale, France87 enrolled5 locationsNCT06711666
Recruiting
Registry for Patients With Lipodystrophy
Lipodystrophy AcquiredLipodystrophy Congenital
University of Ulm5,000 enrolled28 locationsNCT03553420
Recruiting
Congenital Aniridia Patient Questionnaire
Congenital Aniridia
Assistance Publique - Hôpitaux de Paris100 enrolled1 locationNCT05390801
Recruiting
Analysis of Parental Support in Families Using the LENA After Early Cochlear Implantation
Cochlear ImplantationProfound Congenital Deafness
Assistance Publique - Hôpitaux de Paris30 enrolled1 locationNCT05917496
Recruiting
Not Applicable
Prospective Evaluation of OptiThyDose
Graves DiseaseThyroid DiseasesCongenital Hypothyroidism
University Children's Hospital Basel150 enrolled2 locationsNCT06864351
Recruiting
Natural History Study of Children With LAMA2-related Dystrophies
Merosin Deficient Congenital Muscular Dystrophy
Institut de Myologie, France40 enrolled4 locationsNCT06354790
Recruiting
Phase 1Phase 2
A Phase I/II Clinical Trial with SENS-501 in Children Suffering from Severe to Profound Hearing Loss Due to Otoferlin (OTOF) Mutations
Hearing DisordersDeafnessHearing Loss, Sensorineural+5 more
Sensorion12 enrolled2 locationsNCT06370351
Recruiting
Not Applicable
Cardiac Resynchronization Therapy in Adult Congenital Heart Disease With Systemic Right Ventricle: RIGHT-CRT
Congenital Heart DiseaseSystemic Right VentricleCongenitally Corrected Transposition of the Great Arteries+2 more
Assistance Publique - Hôpitaux de Paris40 enrolled13 locationsNCT05524324
Recruiting
Relationship Between Breathing and Attention in Children With Ondine Syndrome
Ondine SyndromeCongenital Central Hypoventilation Syndrome (CCHS)
Assistance Publique - Hôpitaux de Paris20 enrolled1 locationNCT06337149
Recruiting
Not Applicable
OPTImal Treatment of Sinus VENOSUS Defect
Congenital Heart DiseaseSinus Venosus DefectSinus Venosus Atrial Septum Defect
Centre Chirurgical Marie Lannelongue60 enrolled13 locationsNCT05865119
Recruiting
French National Registry of Patients With Tetralogy of Fallot and Implantable Cardioverter Defibrillator
Tetralogy of FallotSudden Cardiac DeathCongenital Heart Disease+2 more
Paris Sudden Death Expertise Center150 enrolled1 locationNCT03837574