Cystinuria Clinical Trials in Philadelphia, Pennsylvania
2 recruitingPhiladelphia, Pennsylvania
Showing 1–2 of 2 trials
Recruiting
Prospective Research Rare Kidney Stones (ProRKS)
Adenine Phosphoribosyltransferase DeficiencyCystinuriaDent Disease+2 more
Mayo Clinic220 enrolled11 locationsNCT02780297
Recruiting
Natural History Study of Homocystinuria Caused by Cystathionine Beta-Synthase Deficiency (ACAPPELLA)
Homocystinuria Due to CBS Deficiency
Travere Therapeutics, Inc.150 enrolled11 locationsNCT02998710