GM1 Clinical Trials in Minneapolis, Minnesota
3 recruitingMinneapolis, Minnesota
Showing 1–3 of 3 trials
Recruiting
Phase 3
A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease, GM1 Gangliosidosis or GM2 Gangliosidosis
GM1 GangliosidosisGM2 GangliosidosisNiemann-Pick Type C Disease
Azafaros A.G.147 enrolled37 locationsNCT07054515
Recruiting
Phase 3
A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of GM1 Gangliosidosis or GM2 Gangliosidosis
Gangliosidoses, GM2Gangliosidosis, GM1
Azafaros A.G.75 enrolled36 locationsNCT07082543
Recruiting
A Natural History Study of the Gangliosidoses
GM1 GangliosidosisGM2 GangliosidosisSandhoff Disease+2 more
University of Minnesota52 enrolled1 locationNCT00668187