LMA Clinical Trials in Barcelona
4 recruitingBarcelona, Spain
Showing 1–4 of 4 trials
Recruiting
Phase 3
REVEAL: A Phase 3 Study of ION582 in Angelman Syndrome
Angelman Syndrome
Ionis Pharmaceuticals, Inc.158 enrolled38 locationsNCT06914609
Recruiting
Lysosomal Acid Lipase (LAL) Deficiency Registry
Lysosomal Acid Lipase DeficiencyWolman DiseaseCholesterol Ester Storage Disease+4 more
Alexion Pharmaceuticals, Inc.300 enrolled104 locationsNCT01633489
Recruiting
Angelman Natural History Study - FAST Spain
Angelman Syndrome
Puerta de Hierro University Hospital40 enrolled2 locationsNCT06115109
Recruiting
Understanding the Long-Term Management of Organic Acidemia Patients With CARBAGLU®: A Mixed Methods Approach
Propionic AcidemiaMethylmalonic Acidemia
RECORDATI GROUP95 enrolled32 locationsNCT04176523