LMA Clinical Trials in Chicago, Illinois
8 recruitingChicago, Illinois
Showing 1–8 of 8 trials
Recruiting
Phase 3
REVEAL: A Phase 3 Study of ION582 in Angelman Syndrome
Angelman Syndrome
Ionis Pharmaceuticals, Inc.158 enrolled38 locationsNCT06914609
Recruiting
Phase 2
A Safety and Efficacy Study of GTX-102 in Subjects With Deletion- or Nondeletion-type Angelman Syndrome (AS)
Angelman Syndrome
Ultragenyx Pharmaceutical Inc60 enrolled22 locationsNCT07157254
Recruiting
Phase 1Phase 2
A Phase 1/2 Study of the Safety and Efficacy of MVX-220 in Angelman Syndrome
Angelman Syndrome
MavriX Bio, LLC12 enrolled3 locationsNCT07181837
Recruiting
Lysosomal Acid Lipase (LAL) Deficiency Registry
Lysosomal Acid Lipase DeficiencyWolman DiseaseCholesterol Ester Storage Disease+4 more
Alexion Pharmaceuticals, Inc.300 enrolled104 locationsNCT01633489
Recruiting
Not Applicable
Web Intervention for Parents of Youth With Genetic Syndromes (WINGS)
Tuberous SclerosisFragile X SyndromeRett Syndrome+5 more
Rush University Medical Center92 enrolled1 locationNCT06139172
Recruiting
Phase 1Phase 2
HALOS: A Safety, Tolerability, Pharmacokinetics and Pharmacodynamics Study of Multiple Ascending Doses of ION582 in Participants With Angelman Syndrome
Angelman Syndrome
Ionis Pharmaceuticals, Inc.70 enrolled11 locationsNCT05127226
Recruiting
An Observational Study of Carbaglu® for the Treatment of MMA and PA in Adults and Pediatrics
Propionic AcidemiaMethylmalonic AcidemiaHyperammonemia
RECORDATI GROUP20 enrolled5 locationsNCT05040178
Recruiting
Angelman Syndrome Natural History Study
Angelman Syndrome
Boston Children's Hospital300 enrolled11 locationsNCT04507997