Phase 2 Muscular Dystrophy Clinical Trials
18 recruitingPhase 2
What is a Phase 2 trial?
Phase 2 trials evaluate whether a treatment works for a specific condition and further assess its safety. These studies typically enroll several hundred participants and provide preliminary data on effectiveness.
Showing 1–18 of 18 trials
Recruiting
Phase 1Phase 2
PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)
Duchenne Muscular Dystrophy With Mutations Amenable to PBGENE-DMD
Precision BioSciences, Inc.18 enrolled1 locationNCT07429240
Recruiting
Phase 2
Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients
Duchenne Muscular DystrophyDMDNeuromuscular Diseases+2 more
Satellos Bioscience, Inc.51 enrolled25 locationsNCT07287189
Recruiting
Phase 1Phase 2
A Phase 1/2 Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of BMN 351 in Participants With Duchenne Muscular Dystrophy
Duchenne Muscular Dystrophy
BioMarin Pharmaceutical18 enrolled8 locationsNCT06280209
Recruiting
Phase 2
A Study to Assess the Efficacy and Safety of Satralizumab in Duchenne Muscular Dystrophy (DMD)
Duchenne Muscular Dystrophy
Hoffmann-La Roche50 enrolled25 locationsNCT06450639
Recruiting
Phase 1Phase 2
A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 45 Skipping to Evaluate the Safety and Efficacy of ENTR-601-45
Duchenne Muscular Dystrophy (DMD)
Entrada Therapeutics, Inc.24 enrolled15 locationsNCT07038824
Recruiting
Phase 1Phase 2
A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 44 Skipping to Evaluate the Safety and Efficacy of ENTR-601-44
Duchenne Muscular Dystrophy (DMD)
Entrada Therapeutics, Inc.24 enrolled14 locationsNCT07037862
Recruiting
Phase 2
NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD)
Duchenne Muscular DystrophyDMDExon 44
NS Pharma, Inc.20 enrolled25 locationsNCT05996003
Recruiting
Phase 1Phase 2
A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
Duchenne Muscular Dystrophy
Solid Biosciences Inc.60 enrolled15 locationsNCT06138639
Recruiting
Phase 1Phase 2
A Study to Evaluate the Safety of AB-1003 (Previously LION-101) in Subjects With Genetic Confirmation of LGMD2I/R9 (Part1)
Muscular DystrophyLimb Girdle Muscular DystrophyLGMD2I+6 more
AskBio Inc10 enrolled6 locationsNCT05230459
Recruiting
Phase 2Phase 3
Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study
Duchenne Muscular Dystrophy
Italfarmaco206 enrolled39 locationsNCT03373968
Recruiting
Phase 1Phase 2
A Study to Evaluate the Safety and Clinical Activity of Intramuscular Doses of BB-301 Administered to Subjects With Oculopharyngeal Muscular Dystrophy With Dysphagia
Oculopharyngeal Muscular Dystrophy
Benitec Biopharma, Inc.30 enrolled1 locationNCT06185673
Recruiting
Phase 2Phase 3
AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD)
Duchenne Muscular Dystrophy
REGENXBIO Inc.65 enrolled17 locationsNCT05693142
Not Yet Recruiting
Phase 2
A Study to Test the Safety and How Well a New Medicine (SAT-3247) Works in Children with Duchenne Muscular Dystrophy Who Can Walk Unassisted – BASECAMP
Duchenne Muscular Dystrophy
Satellos Bioscience, Inc.51 enrolled9 locationsACTRN12625001370493
Recruiting
Phase 1Phase 2
Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53)
Duchenne Muscular Dystrophy
Wave Life Sciences Ltd.26 enrolled5 locationsNCT04906460
Recruiting
Phase 1Phase 2
NS-050/NCNP-03 in Boys With DMD (Meteor50)
Duchenne Muscular Dystrophy
NS Pharma, Inc.20 enrolled18 locationsNCT06053814
Recruiting
Phase 2
Pharmacokinetics and Safety of Givinostat in DMD Patients Ages From at Least 2 Years to Less Then 6 Years Old
Duchenne Muscular Dystrophy
Italfarmaco18 enrolled9 locationsNCT06769633
Recruiting
Phase 2
Vasodilator and Exercise Study for DMD (VASO-REx)
ExerciseDuchenne Muscular DystrophyDMD+4 more
University of Florida50 enrolled1 locationNCT06290713
Completed
Phase 2
A safety and efficacy study of ATL1102 in patients with Duchenne Muscular Dystrophy
Duchenne Muscular Dystrophy
Antisense Therapeutics Limited9 enrolled1 locationACTRN12618000970246